{"id":266943,"date":"2019-05-28T00:17:54","date_gmt":"2019-05-28T07:17:54","guid":{"rendered":"https:\/\/nai500.com\/?p=266943"},"modified":"2019-05-28T00:17:54","modified_gmt":"2019-05-28T07:17:54","slug":"%e4%bb%b7%e5%80%bc%e6%8a%95%e8%b5%84%ef%bc%9a%e6%8a%a4%e5%9f%8e%e6%b2%b3%e6%9c%80%e6%b7%b1%e6%9c%80%e5%ae%bd%e7%9a%843%e5%ae%b6%e5%a4%a7%e5%9e%8b%e7%94%9f%e7%89%a9%e7%a7%91%e6%8a%80%e5%85%ac%e5%8f%b8","status":"publish","type":"post","link":"https:\/\/nai500.com\/zh-hans\/blog\/2019\/05\/%e4%bb%b7%e5%80%bc%e6%8a%95%e8%b5%84%ef%bc%9a%e6%8a%a4%e5%9f%8e%e6%b2%b3%e6%9c%80%e6%b7%b1%e6%9c%80%e5%ae%bd%e7%9a%843%e5%ae%b6%e5%a4%a7%e5%9e%8b%e7%94%9f%e7%89%a9%e7%a7%91%e6%8a%80%e5%85%ac%e5%8f%b8\/","title":{"rendered":"\u4ef7\u503c\u6295\u8d44\uff1a\u62a4\u57ce\u6cb3\u6700\u6df1\u6700\u5bbd\u76843\u5bb6\u5927\u578b\u751f\u7269\u79d1\u6280\u516c\u53f8"},"content":{"rendered":"

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Alexion Pharmaceuticals Inc\uff08NASDAQ: ALXN\uff09<\/h4>\n

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2007\u5e74\uff0c\u7f8e\u56fd\u98df\u54c1\u836f\u54c1\u76d1\u7ba1\u5c40\uff08FDA\uff09\u9996\u6b21\u6279\u51c6Soliris\u6cbb\u7597\u9635\u53d1\u6027\u7761\u7720\u6027\u8840\u7ea2\u86cb\u767d\u5c3f\u75c7\uff08PNH\uff09\u3002\u5230\u76ee\u524d\u4e3a\u6b62\uff0c\u8fd9\u4ecd\u662f\u8fd9\u4e00\u6781\u5ea6\u7f55\u89c1\u9057\u4f20\u6027\u8840\u6db2\u75be\u75c5\u7684\u552f\u4e00\u83b7\u6279\u836f\u7269\u3002\u5728\u6b64\u540e2011\u5e74\u548c2017\u5e74\uff0cSoliris\u4e24\u79cd\u65b0\u7684\u9002\u5e94\u75c7\u2014\u2014\u975e\u5178\u578b\u6eb6\u8840\u6027\u5c3f\u6bd2\u7efc\u5408\u5f81\uff08aHUS\uff09\u4ee5\u53ca\u5168\u8eab\u578b\u91cd\u75c7\u808c\u65e0\u529b\uff08gMG\uff09\u2014\u2014\u4e5f\u5148\u540e\u83b7\u6279\u3002<\/p>\n

\u66f4\u4e3a\u53ef\u559c\u7684\u662f\uff0cAlexion\u53c8\u63a8\u51fa\u4e86\u65b0\u7684\u4ea7\u54c1Ultomiris\u3002\u8be5\u836f\u7269\u7684PNH\u9002\u5e94\u75c7\u5df2\u57282018\u5e7412\u6708\u83b7\u6279\uff0c\u65e9\u4e8e\u9884\u671f\u3002\u6b64\u5916\uff0caHUS\u9002\u5e94\u75c7\u6709\u671b\u5728\u4eca\u5e74\u83b7\u6279\u3002\u5e02\u573a\u7814\u7a76\u516c\u53f8EvaluatePharma\u5c06Ultomiris\u5217\u4e3a2019\u5e74\u7684\u6700\u5927\u65b0\u836f\uff0c\u5e76\u9884\u8ba1\u9500\u552e\u989d\u52302024\u5e74\u5c06\u9ad8\u8fbe$35\u4ebf\u3002<\/p>\n

Biomarin Pharmaceutical Inc\uff08NASDAQ: BMRN\uff09<\/h4>\n

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\u6b64\u5916\uff0cBioMarin\u7684\u5176\u4ed6\u836f\u7269\u4e5f\u62e5\u6709\u62a4\u57ce\u6cb3\u3002Aldurazyme\u662f\u552f\u4e00\u83b7\u6279\u7684MPS I\u6cbb\u7597\u624b\u6bb5\uff0cBrineura\u662f\u552f\u4e00\u83b7\u6279\u7684CLN2\u9176\u66ff\u4ee3\u7597\u6cd5\u3002\u53bb\u5e74\uff0cPalynziq\u83b7\u6279\u6cbb\u7597PKU\u3002<\/p>\n

\u798f\u6cf0\u5236\u836fVertex Pharmaceuticals\uff08NASDAQ: VRTX\uff09<\/h4>\n

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\u4f30\u503c\u6c34\u5e73<\/h4>\n

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