{"id":432556,"date":"2022-08-03T20:37:00","date_gmt":"2022-08-04T03:37:00","guid":{"rendered":"https:\/\/nai500.com\/?p=432556"},"modified":"2022-08-03T20:37:00","modified_gmt":"2022-08-04T03:37:00","slug":"%e9%80%89%e8%82%a1%e7%86%8a%e5%b8%82%e4%b8%ad%e5%93%aa%e4%ba%9b%e6%88%90%e9%95%bf%e8%82%a1%e8%83%bd%e8%83%9c%e5%87%ba","status":"publish","type":"post","link":"https:\/\/nai500.com\/zh-hans\/blog\/2022\/08\/%e9%80%89%e8%82%a1%e7%86%8a%e5%b8%82%e4%b8%ad%e5%93%aa%e4%ba%9b%e6%88%90%e9%95%bf%e8%82%a1%e8%83%bd%e8%83%9c%e5%87%ba\/","title":{"rendered":"\u9009\u80a1\uff1a\u718a\u5e02\u4e2d\u54ea\u4e9b\u6210\u957f\u80a1\u80fd\u80dc\u51fa\uff1f"},"content":{"rendered":"<h2>\u5173\u952e\u70b9<\/h2>\n<ul>\n<li>\u8fd9\u4e2a\u718a\u5e02\u5bf9\u6210\u957f\u80a1\u7684\u6253\u51fb\u5f88\u5927\uff0c\u4f46\u6709\u4e9b\u6210\u957f\u80a1\u8fd8\u662f\u5728\u84ec\u52c3\u53d1\u5c55\u3002<\/li>\n<li>Ionis Pharmaceuticals\u521a\u521a\u7ecf\u5386\u4e86\u4e00\u7cfb\u5217\u7684\u79ef\u6781\u53d1\u5c55\u3002<\/li>\n<li>Jazz Pharmaceuticals\u5728\u6269\u5927\u6d77\u5916\u5e02\u573a\u7684\u540c\u65f6\uff0c\u4e5f\u5728\u589e\u52a0\u7f8e\u56fd\u7684\u9500\u91cf\u3002<\/li>\n<li>\u63a8\u52a8\u8fd9\u4e9b\u80a1\u7968\u6700\u8fd1\u8868\u73b0\u51fa\u8272\u7684\u56e0\u7d20\u4e0d\u6b62\u4e00\u4e2a\u3002<\/li>\n<\/ul>\n<p>\u6295\u8d44\u8005\u89ca\u89ce\u90a3\u4e9b\u5728\u5e02\u573a\u4e0a\u5176\u4ed6\u80a1\u7968\u90fd\u5728\u4e0b\u8dcc\u65f6\u8fd8\u80fd\u6301\u7eed\u6500\u5347\u7684\u80a1\u7968\uff0c\u8fd9\u5e76\u4e0d\u5947\u602a\u3002\u5927\u591a\u6570\u4f01\u4e1a\u5e76\u4e0d\u5177\u5907\u5728\u7ecf\u6d4e\u4e0d\u786e\u5b9a\u65f6\u671f\u8ba9\u80a1\u4e1c\u653e\u5fc3\u7684\u7279\u6b8a\u9171\u6599\uff0c\u800c\u5c11\u6570\u5177\u5907\u8fd9\u79cd\u9171\u6599\u7684\u4f01\u4e1a\u5f88\u53ef\u80fd\u6709\u8feb\u5728\u7709\u776b\u7684\u50ac\u5316\u5242\uff0c\u53ef\u4ee5\u63d0\u9ad8\u6536\u76ca\uff0c\u6216\u8005\u8fdb\u5165\u7ade\u4e89\u5bf9\u624b\u6ca1\u6709\u7684\u8d5a\u94b1\u9886\u57df&#8211;\u6216\u8005\u4e24\u8005\u517c\u800c\u6709\u4e4b\u3002<\/p>\n<p>\u7531\u4e8e\u5373\u5c06\u5230\u6765\u7684\u91cc\u7a0b\u7891\u548c\u5f3a\u52b2\u7684\u76c8\u5229\u8868\u73b0\uff0c\u8fd9\u4e24\u53ea\u751f\u7269\u533b\u836f\u6210\u957f\u80a1\u90fd\u4e3a\u672a\u6765\u7684\u6210\u529f\u505a\u597d\u4e86\u51c6\u5907\uff0c\u6240\u4ee5\u957f\u671f\u6295\u8d44\u8005\u53ef\u80fd\u4f1a\u5bf9\u5b83\u4eec\u611f\u5174\u8da3\u3002<\/p>\n<h2>1. Ionis Pharmaceuticals<\/h2>\n<p>\u53d7\u4e00\u7cfb\u5217\u6709\u5229\u7684\u4e34\u5e8a\u8bd5\u9a8c\u6570\u636e\u548c\u76d1\u7ba1\u673a\u6784\u7684\u6210\u529f\u5f71\u54cd\uff0c\u6210\u957f\u80a1Ionis Pharmaceuticals\uff08<a href=\"https:\/\/nai500.com\/zh-hans\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%af%a2\/?qm_symbol=ONS\">ONS -0.83%<\/a>\uff09\u7684\u80a1\u4ef7\u4eca\u5e74\u4e0a\u6da8\u4e8616%\uff0c\u800c\u5e02\u573a\u5219\u4e0b\u8dcc\u4e8613%\u4ee5\u4e0a\u3002\u867d\u7136\u8be5\u4f01\u4e1a\u6709\u4e09\u79cd\u836f\u54c1\u4e0a\u5e02\uff0c\u5176\u6700\u65b0\u8d22\u5b63\u7684\u6536\u5165\u540c\u6bd4\u589e\u957f27.2%\uff0c\u4f46\u5b83\u51e0\u4e4e\u6ca1\u6709\u76c8\u5229\u3002\u4f46\u662f\uff0c\u7531\u4e8e\u4e00\u4e2a\u7279\u522b\u6709\u5229\u53ef\u56fe\u7684\u9879\u76ee\u63a5\u8fd1\u5176\u5173\u952e\u8bd5\u9a8c\u7684\u5c3e\u58f0\uff0c\u8fd9\u79cd\u60c5\u51b5\u53ef\u80fd\u5f88\u5feb\u5c31\u4f1a\u6539\u53d8\u3002<\/p>\n<p>6\u670821\u65e5\uff0c\u8be5\u516c\u53f8\u5ba3\u5e03\u5176\u8c03\u67e5\u5019\u9009\u836f\u7269eplontersen\u76843\u671f\u4e34\u5e8a\u8bd5\u9a8c\u7684\u4e2d\u671f\u5206\u6790\u8fbe\u5230\u4e86\u8be5\u7814\u7a76\u7684\u4e24\u4e2a\u4e3b\u8981\u7ec8\u70b9\u3002\u8fd9\u610f\u5473\u7740\u5b83\u7ee7\u7eed\u83b7\u5f97\u76d1\u7ba1\u673a\u6784\u6279\u51c6\u7684\u673a\u4f1a\u76f8\u5f53\u5927\u3002Ionis\u5e0c\u671b\u5728\u4eca\u5e74\u665a\u4e9b\u65f6\u5019\u5411\u7f8e\u56fd\u98df\u54c1\u836f\u54c1\u76d1\u7763\u7ba1\u7406\u5c40\uff08FDA\uff09\u63d0\u4ea4\u4e00\u4efd\u65b0\u836f\u7533\u8bf7\uff08NDA\uff09\u3002Eplontersen\u6b63\u5728\u88ab\u8c03\u67e5\u5176\u5728\u6cbb\u7597\u9057\u4f20\u6027\u8f6c\u7532\u72b6\u817a\u7d20\u4ecb\u5bfc\u7684\u6dc0\u7c89\u6837\u591a\u53d1\u6027\u795e\u7ecf\u75c5\u53d8\uff08ATTRv-PN\uff09\u65b9\u9762\u7684\u4f18\u70b9\uff0c\u8fd9\u662f\u4e00\u79cd\u7f55\u89c1\u7684\u4e25\u91cd\u6162\u6027\u75be\u75c5\u3002<\/p>\n<p>\u5bf9\u6295\u8d44\u8005\u6765\u8bf4\uff0c\u6700\u91cd\u8981\u7684\u662f\uff0c\u7ba1\u7406\u5c42\u8ba4\u4e3a\uff0c\u5728\u9500\u552e\u9ad8\u5cf0\u671f\uff0ceplontersen\u7684\u5546\u4e1a\u5316\u4ef7\u503c\u5c06\u8fbe\u5230\u6bcf\u5e74\u6570\u5341\u4ebf\u7f8e\u5143\uff0ceplontersen\u7684\u8d21\u732e\u53ef\u80fd\u662f\u5de8\u5927\u7684\u3002<\/p>\n<p>\u540c\u65f6\uff0c\u8be5\u516c\u53f8\u7684\u4e00\u4e9b\u65e9\u671f\u9879\u76ee\u4e5f\u5728\u987a\u5229\u8fdb\u884c\u30026\u670813\u65e5\uff0c\u7f8e\u56fd\u98df\u54c1\u836f\u54c1\u76d1\u7763\u7ba1\u7406\u5c40\u7684\u76d1\u7ba1\u673a\u6784\u6388\u4e88Ionis Pharmaceuticals\u540d\u4e3aION582\u7684\u5019\u9009\u836f\u7269\u7684\u5b64\u513f\u836f\u8d44\u8d28\uff0c\u8be5\u836f\u7269\u65e8\u5728\u6cbb\u7597\u7f55\u89c1\u7684\u9057\u4f20\u6027\u75be\u75c5Angelman\u7efc\u5408\u5f81\u30027\u670828\u65e5\uff0c\u8be5\u516c\u53f8\u5ba3\u5e03\u4e86\u5176\u79f0\u4e3afesomersen\u6297\u51dd\u8840\u6cbb\u7597\u65b9\u6cd5\u76842b\u671f\u8bd5\u9a8c\u7684\u79ef\u6781\u7ed3\u679c\u3002<\/p>\n<h2>2. 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