{"id":452555,"date":"2023-02-17T23:37:49","date_gmt":"2023-02-18T07:37:49","guid":{"rendered":"https:\/\/nai500.com\/?p=452555"},"modified":"2023-02-17T23:37:49","modified_gmt":"2023-02-18T07:37:49","slug":"%e5%9f%ba%e5%9b%a0%e7%bc%96%e8%be%91%e6%8a%80%e6%9c%af%e6%80%8e%e4%b9%88%e6%a0%b7%e6%88%96%e5%b0%86%e5%9c%a8%e7%89%9b%e5%b8%82%e4%b8%ad%e6%bc%94%e7%bb%8e%e6%96%b0%e7%a5%9e%e8%af%9d","status":"publish","type":"post","link":"https:\/\/nai500.com\/zh-hans\/blog\/2023\/02\/%e5%9f%ba%e5%9b%a0%e7%bc%96%e8%be%91%e6%8a%80%e6%9c%af%e6%80%8e%e4%b9%88%e6%a0%b7%e6%88%96%e5%b0%86%e5%9c%a8%e7%89%9b%e5%b8%82%e4%b8%ad%e6%bc%94%e7%bb%8e%e6%96%b0%e7%a5%9e%e8%af%9d\/","title":{"rendered":"\u57fa\u56e0\u7f16\u8f91\u6280\u672f\u600e\u4e48\u6837\uff1f\u6216\u5c06\u5728\u725b\u5e02\u4e2d\u6f14\u7ece\u65b0\u795e\u8bdd"},"content":{"rendered":"<ul>\n<li>\u725b\u5e02\u5f80\u5f80\u5bf9\u76c8\u5229\u524d\u7684\u751f\u7269\u79d1\u6280\u516c\u53f8\u6709\u5229\u3002<\/li>\n<li>CRISPR Therapeutics\u53ef\u80fd\u4f1a\u5728\u4e00\u5e74\u5185\u63a8\u51fa\u4e00\u79cd\u65b0\u836f\u3002<\/li>\n<li>Editas Medicine\u6b63\u5728\u52aa\u529b\u4e0eCRISPR Therapeutics\u7ade\u4e89\u3002<\/li>\n<\/ul>\n<p>\u4ed6\u4eec\u90fd\u5904\u4e8e\u57fa\u56e0\u7f16\u8f91\u6280\u672f\u7684\u524d\u6cbf\u3002<\/p>\n<p>\u5927\u591a\u6570\u6295\u8d44\u8005\u90fd\u77e5\u9053\uff0c\u751f\u7269\u79d1\u6280\u80a1\u5f88\u5bb9\u6613\u4e00\u98de\u51b2\u5929\u6216\u8005\u8dcc\u5165\u8c37\u5e95\u3002\u4f46\u5f53\u5e02\u573a\u98d9\u5347\u3001\u4e50\u89c2\u60c5\u7eea\u9ad8\u6da8\u65f6\uff0c\u4e00\u4e9b\u751f\u7269\u79d1\u6280\u80a1\u7684\u6da8\u5e45\u751a\u81f3\u53ef\u80fd\u6bd4\u5e73\u65f6\u66f4\u9ad8\uff0c\u8fd9\u610f\u5473\u7740\u5728\u5e02\u573a\u884c\u60c5\u75b2\u8f6f\u65f6\u4e70\u5165\u5b83\u4eec\u7684\u6295\u8d44\u8005\u6709\u673a\u4f1a\u83b7\u5229\uff0c\u5c31\u50cf\u73b0\u5728\u4e00\u6837\u3002<\/p>\n<p>\u5982\u679c\u672a\u6765\u51e0\u5e74\u51fa\u73b0\u725b\u5e02\uff0c\u8fd9\u4e24\u5bb6\u57fa\u56e0\u7f16\u8f91\u751f\u7269\u79d1\u6280\u516c\u53f8\u53ef\u80fd\u4f1a\u6709\u8fd9\u79cd\u6548\u679c\u3002\u8ba9\u6211\u4eec\u770b\u770b\u4e3a\u4ec0\u4e48\u3002<\/p>\n<h2>1. CRISPR Therapeutics<\/h2>\n<p>\u5c3d\u7ba1\u76ee\u524d\u6ca1\u6709\u4efb\u4f55\u7ecf\u5e38\u6027\u6536\u5165\uff0c\u4f46<a href=\"https:\/\/nai500.com\/zh-hans\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%af%a2\/?qm_symbol=CRSP\">CRISPR Therapeutics(CRSP)<\/a>\u9884\u8ba1\u57282023\u5e74\u4f1a\u51fa\u73b0\u4e00\u4e9b\u50ac\u5316\u5242\u3002\u6700\u91cd\u8981\u7684\u50ac\u5316\u5242\u5c06\u662f\u76d1\u7ba1\u673a\u6784\u5bf9\u5019\u9009\u836f\u7269exa-cel\u5728\u7f8e\u56fd\u7684\u751f\u7269\u5236\u5242\u8bb8\u53ef\u7533\u8bf7(BLA)\u7684\u56de\u5e94\uff0c\u8be5\u516c\u53f8\u8ba1\u5212\u5728\u7b2c\u4e00\u5b63\u5ea6\u672b\u4e4b\u524d\u63d0\u4ea4\u76f8\u5173\u7533\u8bf7\u3002<\/p>\n<p>Exa-cel\u662f\u4e00\u79cd\u7ec6\u80de\u7597\u6cd5\uff0c\u4f7f\u7528\u57fa\u56e0\u5de5\u7a0b\u8840\u7ec6\u80de\u6cbb\u7597\u9057\u4f20\u6027\u75be\u75c5\uff0c\u5373\u03b2\u5730\u4e2d\u6d77\u8d2b\u8840\u548c\u9570\u72b6\u7ec6\u80de\u75c5\u3002\u8be5\u516c\u53f8\u7684\u4e34\u5e8a\u8bd5\u9a8c\u6570\u636e\u8868\u660e\uff0cExa-cel\u53ef\u80fd\u662f\u5927\u591a\u6570\u60a3\u6709\u8fd9\u4e9b\u75be\u75c5\u7684\u60a3\u8005\u7684\u6cbb\u6108\u65b9\u6cd5\u3002\u76d1\u7ba1\u673a\u6784\u53ef\u80fd\u4f1a\u5728\u5e74\u5e95\u524d\u505a\u51fa\u5ba1\u6279\uff0c\u4f46\u66f4\u6709\u53ef\u80fd\u57282024\u5e74\u521d\u8fdb\u884c\u3002<\/p>\n<p>CRISPR Therapeutics\u6700\u7ec8\u5c06\u4e0e\u5408\u4f5c\u65b9Vertex Pharmaceuticals\u5206\u644a\u836f\u7269\u9500\u552e\u7684\u4efb\u4f55\u6210\u672c\u548c\u5229\u6da6\u3002\u7531\u4e8e\u7f8e\u56fd\u548c\u6b27\u76df\u76ee\u524d\u53ea\u6709\u5927\u7ea630,000\u540d\u6f5c\u5728\u60a3\u8005\uff0c\u5982\u679c\u4e0d\u8fdb\u884c\u4e00\u4e9b\u989d\u5916\u7684\u5f00\u53d1\u5de5\u4f5c\u6765\u6269\u5c55Exa-cel\u7684\u6cbb\u7597\u529f\u80fd\uff0cexa-cel\u5c31\u4e0d\u53ef\u80fd\u6709\u4e00\u4e2a\u5de8\u5927\u800c\u6301\u4e45\u7684\u5e02\u573a\u3002<\/p>\n<p>\u5982\u679c\u5728exa-cel\u83b7\u5f97\u6279\u51c6\u65f6\u5b58\u5728\u6301\u7eed\u7684\u725b\u5e02\uff0c\u90a3\u4e48\u8be5\u516c\u53f8\u7684\u80a1\u4ef7\u5c06\u5f97\u5230\u8fdb\u4e00\u6b65\u63d0\u632f\u3002\u8fd9\u662f\u65e9\u665a\u8d2d\u4e70\u8be5\u80a1\u7684\u53e6\u4e00\u4e2a\u5408\u7406\u7406\u7531\u3002<\/p>\n<h2>2. Editas Medicine<\/h2>\n<p><a href=\"https:\/\/nai500.com\/zh-hans\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%af%a2\/?qm_symbol=EDIT\">Editas Medicine(EDIT)<\/a>\u80a1\u4ef7\u6709\u5f88\u5927\u7684\u673a\u4f1a\u5728\u4e0b\u4e00\u4e2a\u725b\u5e02\u4e2d\u8dc3\u5347\u3002<\/p>\n<p>\u901a\u8fc7\u4e0e\u767e\u65f6\u7f8e\u65bd\u8d35\u5b9d\u5408\u4f5c\uff0cEditas\u6b63\u5728\u5bfb\u6c42\u65e8\u5728\u6cbb\u7597\u9570\u72b6\u7ec6\u80de\u75c5\u548c\u03b2\u5730\u4e2d\u6d77\u8d2b\u8840\u7684\u57fa\u56e0\u7597\u6cd5\uff0c\u4f46\u90fd\u5904\u4e8e\u65e9\u671f\u4e34\u5e8a\u8bd5\u9a8c\u9636\u6bb5\u3002\u5728\u672a\u6765\u51e0\u5e74\uff0cEditas Medicine\u5c06\u8bc1\u660e\u8be5\u516c\u53f8\u7684\u7597\u6cd5\u4e0eCRISPR\u7597\u6cd5\u7684\u4e0d\u540c\u4e4b\u5904\u3002<\/p>\n<p>\u5982\u679c\u8be5\u516c\u53f8\u63a8\u8fdb\u57fa\u56e0\u7f16\u8f91\u65b9\u6cd5\u4ee5\u6cbb\u6108\u6216\u51cf\u8f7b\u9057\u4f20\u75c5\u75c7\u7684\u4e34\u5e8a\u524d\u9879\u76ee\uff0c\u90a3\u5c06\u662f\u4e00\u4e2a\u66f4\u5927\u7684\u50ac\u5316\u5242\u3002\u76ee\u524d\uff0c\u5c1a\u4e0d\u6e05\u695a\u8be5\u516c\u53f8\u6b63\u5728\u8003\u8651\u6cbb\u7597\u54ea\u4e9b\u75be\u75c5\uff0c\u56e0\u6b64\u8fd9\u4e9b\u7597\u6cd5\u4e0d\u592a\u53ef\u80fd\u5f88\u5feb\u5bf9\u8d22\u52a1\u4e1a\u7ee9\u505a\u51fa\u4efb\u4f55\u8d21\u732e\uff0c\u4f46\u4efb\u4f55\u4e34\u5e8a\u8fdb\u5c55\u90fd\u5c06\u662f\u4e00\u4e2a\u7a81\u7834\u3002<\/p>\n<p>Editas\u9884\u8ba1\u6709\u8db3\u591f\u7684\u73b0\u91d1\u751f\u5b58\u52302025\u5e74\uff0c4.196\u4ebf\u7f8e\u5143\u7684\u50a8\u5907\u4e5f\u63d0\u4f9b\u4e86\u8db3\u591f\u7684\u7075\u6d3b\u6027\uff0c\u4ee5\u4fbf\u5728\u9700\u8981\u65f6\u6536\u8d2d\u8f83\u5c0f\u7684\u4f01\u4e1a\u3002<\/p>\n<p>\u4e0d\u80fd\u4fdd\u8bc1\u8be5\u516c\u53f8\u4e00\u5b9a\u4f1a\u6210\u529f\uff0c\u4f46\u5728\u672a\u6765\u51e0\u5e74\u5185\u53d6\u5f97\u4e00\u4e9b\u80dc\u5229\u80af\u5b9a\u4f1a\u9f13\u821e\u6295\u8d44\u8005\uff0c\u5c24\u5176\u662f\u5728\u725b\u5e02\u4e2d\u3002<\/p>\n<p>CRISPR Therapeutics\u548cEditas Medicine\u5728\u672a\u6765\u51e0\u5e74\u90fd\u5177\u6709\u5de8\u5927\u7684\u6f5c\u529b\uff0c\u524d\u63d0\u662f\u60a8\u53ef\u4ee5\u627f\u53d7\u6295\u8d44\u751f\u7269\u79d1\u6280\u80a1\u7968\u7684\u5de8\u5927\u98ce\u9669\u3002<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\u725b\u5e02\u5f80\u5f80\u5bf9\u76c8\u5229\u524d\u7684\u751f\u7269\u79d1\u6280\u516c\u53f8\u6709\u5229\u3002 CRISPR Therapeutics\u53ef\u80fd\u4f1a\u5728\u4e00\u5e74\u5185\u63a8\u51fa\u4e00\u79cd\u65b0\u836f\u3002 Ed [&hellip;]<\/p>\n","protected":false},"author":9,"featured_media":452556,"comment_status":"closed","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"footnotes":"","_links_to":"","_links_to_target":""},"categories":[427],"tags":[820,455,925,459],"class_list":["post-452555","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-market-news-zh-hans","tag-820","tag-455","tag-925","tag-459","sectors-life-science-zh-hans","locations-us-zh-hans","exchange-nasdaq-zh-hans","exchange-nyse-zh-hans"],"acf":[],"_links":{"self":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts\/452555","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/users\/9"}],"replies":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/comments?post=452555"}],"version-history":[{"count":0,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts\/452555\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/media\/452556"}],"wp:attachment":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/media?parent=452555"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/categories?post=452555"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/tags?post=452555"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}