{"id":465244,"date":"2023-06-28T01:23:48","date_gmt":"2023-06-28T08:23:48","guid":{"rendered":"https:\/\/nai500.com\/?p=465244"},"modified":"2023-06-28T01:41:10","modified_gmt":"2023-06-28T08:41:10","slug":"%e5%85%b3%e9%94%ae%e5%82%ac%e5%8c%96%e5%89%82%e5%8d%b3%e5%b0%86%e6%9d%a5%e4%b8%b4%e8%bf%99%e4%ba%9b%e5%88%b6%e8%8d%af%e8%82%a1%e5%be%88%e5%8f%af%e8%83%bd%e6%9a%b4%e6%b6%a8","status":"publish","type":"post","link":"https:\/\/nai500.com\/zh-hans\/blog\/2023\/06\/%e5%85%b3%e9%94%ae%e5%82%ac%e5%8c%96%e5%89%82%e5%8d%b3%e5%b0%86%e6%9d%a5%e4%b8%b4%e8%bf%99%e4%ba%9b%e5%88%b6%e8%8d%af%e8%82%a1%e5%be%88%e5%8f%af%e8%83%bd%e6%9a%b4%e6%b6%a8\/","title":{"rendered":"\u5173\u952e\u50ac\u5316\u5242\u5373\u5c06\u6765\u4e34\uff0c\u8fd9\u4e9b\u5236\u836f\u80a1\u5f88\u53ef\u80fd\u66b4\u6da8"},"content":{"rendered":"<ul>\n<li>\u5f53\u5173\u952e\u8bd5\u9a8c\u5931\u8d25\u65f6\uff0cBridgeBio\u80a1\u7968\u66b4\u8dcc\uff0c\u4f46\u540e\u7eed\u6570\u636e\u53ef\u80fd\u4f1a\u8ba9\u8be5\u9879\u76ee\u548c\u6295\u8d44\u8005\u5f97\u5230\u56de\u62a5\u3002<\/li>\n<li>\u5982\u679c\u7f8e\u56fd\u98df\u54c1\u836f\u54c1\u76d1\u7763\u7ba1\u7406\u5c40\u53d7\u7406\u65b0\u836f\u7533\u8bf7\uff0cBiohaven\u80a1\u4ef7\u53ef\u80fd\u4f1a\u98d9\u5347\u3002<\/li>\n<\/ul>\n<p>\u60a8\u662f\u5426\u6b63\u5728\u5bfb\u627e\u53ef\u4ee5\u5728\u77ed\u65f6\u95f4\u5185\u5927\u5e45\u6ce2\u52a8\u7684\u80a1\u7968\uff1f\u90a3\u4e48\u8fd9\u4e24\u53ea\u62e5\u6709\u5de8\u5927\u50ac\u5316\u5242\u7684\u5236\u836f\u80a1\u7edd\u5bf9\u503c\u5f97\u4f60\u5173\u6ce8\u3002\u5230\u4e03\u6708\u5e95\uff0c\u8fd9\u4e9b\u516c\u53f8\u9884\u8ba1\u5c06\u53d1\u5e03\u4e00\u4e9b\u91cd\u8981\u516c\u544a\u3002\u79ef\u6781\u7684\u7ed3\u679c\u53ef\u80fd\u4f1a\u8ba9\u8fd9\u4e9b\u80a1\u7968\u80a1\u4ef7\u4e00\u591c\u4e4b\u95f4\u4e0a\u6da8\u4e00\u500d\u4ee5\u4e0a\u3002\u7136\u800c\uff0c\u5982\u679c\u7ed3\u679c\u4ee4\u4eba\u5931\u671b\uff0c\u80a1\u4ef7\u53ef\u80fd\u4f1a\u4e0b\u8dcc\u3002\u5728\u76f2\u76ee\u5730\u62ff\u81ea\u5df1\u8f9b\u82e6\u8d5a\u6765\u7684\u94b1\u5192\u9669\u4e4b\u524d\uff0c\u8ba9\u6211\u4eec\u5148\u770b\u770b\u53ef\u4ee5\u8ba9\u8fd9\u4e24\u5bb6\u516c\u53f8\u80a1\u4ef7\u4e0a\u6da8\u7684\u50ac\u5316\u5242\u3002<\/p>\n<h2>1. BridgeBio<\/h2>\n<p><a href=\"https:\/\/nai500.com\/zh-hans\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%af%a2\/?qm_symbol=BBIO\">BridgeBio (BBIO)<\/a>\u662f\u4e00\u5bb6\u5904\u4e8e\u5546\u4e1a\u9636\u6bb5\u7684\u5236\u836f\u5546\uff0c\u6709\u4e00\u79cd\u5728\u552e\u836f\u7269\u3002Nulibry\u65e9\u57282021\u5e74\u5c31\u83b7\u5f97\u4e86\u6cbb\u7597A\u578b\u94bc\u8f85\u56e0\u5b50\u7f3a\u4e4f\u75c7\uff08\u4e00\u79cd\u6781\u5176\u7f55\u89c1\u7684\u75be\u75c5\uff09\u7684\u6279\u51c6\u3002\u4e0d\u5e78\u7684\u662f\uff0c\u9500\u552e\u60c5\u51b5\u5e76\u4e0d\u90a3\u4e48\u4ee4\u4eba\u5174\u594b\u3002\u7531\u4e8e\u9700\u8981\u6cbb\u7597\u7684\u6f5c\u5728\u60a3\u8005\u4e0d\u5230150\u540d\uff0cNulibry\u7684\u9500\u552e\u989d\u975e\u5e38\u4f4e\uff0c\u4ee5\u81f3\u4e8e\u8be5\u516c\u53f8\u7684\u8d22\u5b63\u6536\u76ca\u62a5\u544a\u751a\u81f3\u6ca1\u6709\u63d0\u53ca\u8fd9\u4e00\u70b9\u3002<\/p>\n<p>BridgeBio\u9884\u8ba1\u5c06\u4e8e7\u6708\u5e95\u516c\u5e03acoramidis\uff08\u4e00\u79cd\u53e3\u670d\u8f6c\u7532\u72b6\u817a\u7d20\u86cb\u767d\u52a8\u529b\u7a33\u5b9a\u5242\uff09\u76843\u671f\u8bd5\u9a8c\u7ed3\u679c\u3002\u8f6c\u7532\u72b6\u817a\u7d20\u86cb\u767d\u4ecb\u5bfc\u7684\u5fc3\u808c\u75c5\uff08ATTR-CM\uff09\u662f\u4e00\u79cd\u7f55\u89c1\u75be\u75c5\u3002\u4e0d\u8fc7\uff0c\u8f89\u745e\u7684ATTR-CM\u6cbb\u7597\u836f\u7269Vyndaqel\u5df2\u7ecf\u662f\u4e00\u79cd\u91cd\u78c5\u836f\u7269\uff0c\u5e74\u9500\u552e\u989d\u8fbe27\u4ebf\u7f8e\u5143\u3002Acoramidis\u5df2\u88ab\u8bc1\u660e\u53ef\u4ee5\u7a33\u5b9a\u8f6c\u7532\u72b6\u817a\u7d20\u86cb\u767d\u3002<\/p>\n<p>\u76ee\u524d\uff0cBridgeBio\u7684\u5e02\u503c\u4e3a25\u4ebf\u7f8e\u5143\uff0c\u800cacoramidis\u53ea\u662f\u5904\u4e8e\u540e\u671f\u4e34\u5e8a\u8bd5\u9a8c\u7684\u4e24\u79cd\u836f\u7269\u4e4b\u4e00\u3002\u6709\u4e86\u5e9e\u5927\u7684\u7ba1\u7ebf\uff0c\u5373\u4f7facoramidis\u518d\u6b21\u5931\u8d25\uff0cBridgeBio\u4e5f\u53ef\u4ee5\u7ee7\u7eed\u6218\u6597\u3002\u8fd9\u53ea\u80a1\u7968\u770b\u8d77\u6765\u975e\u5e38\u9002\u5408\u5177\u6709\u9ad8\u98ce\u9669\u627f\u53d7\u80fd\u529b\u7684\u6295\u8d44\u8005\u3002<\/p>\n<h2>2. Biohaven<\/h2>\n<p><a href=\"https:\/\/nai500.com\/zh-hans\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%af%a2\/?qm_symbol=BHVN\">Biohaven (BHVN)<\/a>\u662f\u4e00\u5bb6\u4e34\u5e8a\u9636\u6bb5\u7684\u5236\u836f\u5546\uff0c\u6ca1\u6709\u4efb\u4f55\u6279\u51c6\u7684\u4ea7\u54c1\u53ef\u4f9b\u9500\u552e\u3002\u4e0d\u8fc7\uff0c\u5728\u653e\u5f03\u4e4b\u524d\uff0c\u6295\u8d44\u8005\u5e94\u8be5\u77e5\u9053\u8be5\u516c\u53f8\u6709\u80fd\u529b\u8ba9\u65b0\u836f\u901a\u8fc7\u76d1\u7ba1\u5ba1\u6279\u3002\u53bb\u5e7410\u6708\uff0c\u8f89\u745e\u4ee5116\u4ebf\u7f8e\u5143\u4eceBiohaven\u6536\u8d2d\u4e86\u4e24\u79cd\u6025\u6027\u504f\u5934\u75db\u6cbb\u7597\u836f\u7269Nurtec\u548cZavzpret\u3002<\/p>\n<p>Biohaven\u62e5\u6709\u5f3a\u5927\u7684\u9488\u5bf9\u795e\u7ecf\u7cfb\u7edf\u75be\u75c5\u7684\u4e34\u5e8a\u9636\u6bb5\u5019\u9009\u836f\u7269\u4ea7\u54c1\u7ebf\u3002\u8be5\u516c\u53f8\u76ee\u524d\u6700\u5148\u8fdb\u7684\u65b0\u5019\u9009\u836f\u7269\u662ftroriluzole\uff0c\u8fd9\u662f\u4e00\u79cd\u6cbb\u7597\u810a\u9ad3\u5c0f\u8111\u6027\u5171\u6d4e\u5931\u8c03\uff08SCA\uff09\u548c\u5f3a\u8feb\u75c7\u7684\u5b9e\u9a8c\u6027\u6cbb\u7597\u836f\u7269\u3002<\/p>\n<p>\u4eca\u5e745\u6708\uff0cBiohaven\u5411FDA\u63d0\u4ea4\u4e86\u4e00\u4efd\u5173\u4e8etroriluzole\u6cbb\u75973\u578bSCA\u7684\u65b0\u836f\u7533\u8bf7\uff0c\u8fd9\u79cd\u75be\u75c5\u5f71\u54cd\u5317\u7f8e\u3001\u6b27\u6d32\u548c\u65e5\u672c\u7ea610,600\u4eba\u3002\u6211\u4eec\u4ecd\u7136\u4e0d\u77e5\u9053\u7f8e\u56fd\u98df\u54c1\u836f\u54c1\u76d1\u7763\u7ba1\u7406\u5c40(FDA)\u662f\u5426\u4f1a\u6279\u51c6\u8be5\u7533\u8bf7\u3002\u4e00\u65e6\u63d0\u4ea4\u65b0\u836f\u7533\u8bf7\uff0cFDA\u9700\u8981\u4e24\u4e2a\u6708\u7684\u65f6\u95f4\u8981\u6c42\u63d0\u4f9b\u66f4\u591a\u6570\u636e\u6216\u5f00\u59cb\u901a\u5e38\u957f\u8fbe10\u4e2a\u6708\u7684\u5ba1\u67e5\u8fc7\u7a0b\u3002Biohaven\u76ee\u524d\u7684\u5e02\u503c\u4ec5\u4e3a15\u4ebf\u7f8e\u5143\uff0c\u56e0\u4e3a\u6295\u8d44\u8005\u4e0d\u786e\u5b9aFDA\u5c06\u5982\u4f55\u5904\u7406\u8be5\u7533\u8bf7\u3002<\/p>\n<p>\u5c3d\u7ba1\u8fd9\u4e24\u53ea\u751f\u7269\u79d1\u6280\u80a1\u90fd\u6709\u53ef\u80fd\u8ba9\u80a1\u4ef7\u98d9\u5347\u7684\u50ac\u5316\u5242\uff0c\u4f46\u4ecd\u6709\u5f88\u591a\u95ee\u9898\u53ef\u80fd\u4f1a\u51fa\u73b0\u3002\u5982\u679c\u60a8\u6253\u7b97\u5728BridgeBio\u6216Biohaven\u4e0a\u5192\u9669\uff0c\u8bf7\u52a1\u5fc5\u8ba9\u5b83\u4eec\u5728\u4f60\u7684\u591a\u5143\u5316\u6295\u8d44\u7ec4\u5408\u4e2d\u5360\u636e\u76f8\u5bf9\u8f83\u5c0f\u7684\u6bd4\u4f8b\u3002<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\u5f53\u5173\u952e\u8bd5\u9a8c\u5931\u8d25\u65f6\uff0cBridgeBio\u80a1\u7968\u66b4\u8dcc\uff0c\u4f46\u540e\u7eed\u6570\u636e\u53ef\u80fd\u4f1a\u8ba9\u8be5\u9879\u76ee\u548c\u6295\u8d44\u8005\u5f97\u5230\u56de\u62a5\u3002 \u5982\u679c\u7f8e\u56fd\u98df\u54c1\u836f\u54c1\u76d1\u7763 [&hellip;]<\/p>\n","protected":false},"author":9,"featured_media":465246,"comment_status":"closed","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"footnotes":"","_links_to":"","_links_to_target":""},"categories":[427],"tags":[455,925,459],"class_list":["post-465244","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-market-news-zh-hans","tag-455","tag-925","tag-459","sectors-life-science-zh-hans","locations-us-zh-hans","exchange-nasdaq-zh-hans","exchange-nyse-zh-hans"],"acf":[],"_links":{"self":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts\/465244","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/users\/9"}],"replies":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/comments?post=465244"}],"version-history":[{"count":0,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts\/465244\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/media\/465246"}],"wp:attachment":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/media?parent=465244"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/categories?post=465244"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/tags?post=465244"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}