{"id":493763,"date":"2024-04-10T00:23:05","date_gmt":"2024-04-10T07:23:05","guid":{"rendered":"https:\/\/nai500.com\/?p=493763"},"modified":"2024-04-10T00:23:05","modified_gmt":"2024-04-10T07:23:05","slug":"%e5%88%9b%e6%96%b0-%e5%8c%bb%e7%96%97%e6%88%90%e9%95%bf%e8%82%a1-%e6%96%b0%e7%9a%84%e9%87%8d%e7%a3%85%e8%8d%af-%e4%b8%8a%e5%b8%82","status":"publish","type":"post","link":"https:\/\/nai500.com\/zh-hans\/blog\/2024\/04\/%e5%88%9b%e6%96%b0-%e5%8c%bb%e7%96%97%e6%88%90%e9%95%bf%e8%82%a1-%e6%96%b0%e7%9a%84%e9%87%8d%e7%a3%85%e8%8d%af-%e4%b8%8a%e5%b8%82\/","title":{"rendered":"\u521b\u65b0\u4e0d\u6b62\uff0c\u8fd9\u53ea\u533b\u7597\u6210\u957f\u80a1\u65b0\u7684\u91cd\u78c5\u836f\u8ddd\u79bb\u4e0a\u5e02\u53c8\u8fd1\u4e86\u4e00\u6b65"},"content":{"rendered":"<p>\u751f\u7269\u79d1\u6280\u5de8\u5934<a href=\"https:\/\/nai500.com\/zh-hans\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%af%a2\/?qm_symbol=VRTX\">\u798f\u6cf0\u5236\u836fVertex Pharmaceuticals\uff08NASDAQ:VRTX\uff09<\/a>\u5c31\u662f\u4e00\u53f0\u4e0d\u65ad\u5411\u524d\u7684\u521b\u65b0\u673a\u5668\u3002\u8fc7\u53bb6\u4e2a\u6708\uff0c\u8be5\u516c\u53f8\u4e0a\u5e02\u4e86\u5168\u65b0\u4e14\u6781\u6709\u524d\u666f\u7684\u4ea7\u54c1\uff0c\u540c\u65f6\u53d1\u5e03\u4e86\u5019\u9009\u4ea7\u54c1\u79ef\u6781\u7684\u4e09\u671f\u8bd5\u9a8c\u7ed3\u679c\u3002\u4e0d\u8fc7\uff0c\u8be5\u5236\u836f\u5546\u7684\u521b\u65b0\u5e76\u672a\u6b62\u6b65\uff0c\u516c\u53f8\u53e6\u4e00\u6b3e\u65b0\u7684\u6f5c\u529b\u91cd\u78c5\u836f\u8ddd\u79bb\u4e0a\u5e02\u53c8\u8fd1\u4e86\u4e00\u6b65\u3002<\/p>\n<p>\u4e0d\u8fc7\u5728\u6b64\u4e4b\u524d\uff0c\u6211\u4eec\u5148\u6765\u8bf4\u8bf4\u798f\u6cf0\u5236\u836f\u7684\u6210\u529f\u6545\u4e8b\u3002<\/p>\n<p>\u8fc7\u53bb10\u5e74\uff0c\u8be5\u751f\u7269\u79d1\u6280\u516c\u53f8\u4e3b\u653b\u4e00\u4e2a\u7ec6\u5206\u9886\u57df\uff1a\u56ca\u6027\u7ea4\u7ef4\u5316\uff08CF\uff09\u3002\u5728\u798f\u6cf0\u5236\u836f\u53d6\u5f97\u7a81\u7834\u4e4b\u524d\uff0c\u5e02\u573a\u4e0a\u6ca1\u6709\u4e00\u6b3e\u836f\u7269\u80fd\u591f\u6cbb\u7597\u8fd9\u79cd\u80ba\u90e8\u7684\u7f55\u89c1\u75c5\u3002\u51ed\u501fTrikafta\u3001Kalydeco\u3001Orkambi\u548cSymdeko\u7b49CF\u836f\u7269\uff0c\u8be5\u516c\u53f8\u73b0\u5728\u5df2\u7ecf\u53d1\u5c55\u4e3a\u4e00\u5bb6\u5e9e\u5927\u7684\u751f\u7269\u6280\u672f\u516c\u53f8\uff0c\u5e02\u503c\u8d85\u8fc7\u5343\u4ebf\u7f8e\u5143\uff0c\u5e74\u8425\u6536\u767e\u4ebf\u7f8e\u91d1\uff0c\u5e76\u4e14\u5728CF\u6cbb\u7597\u9886\u57df\u5360\u636e\u4e86\u72ec\u5360\u5730\u4f4d\u3002<\/p>\n<p>\u4e0d\u8fc7\uff0c\u798f\u6cf0\u5236\u836f\u4e5f\u5728\u79ef\u6781\u62d3\u5c55\u65b0\u7684\u6cbb\u7597\u9886\u57df\uff0c\u6bd4\u5982\u8bf4\u6cbb\u7597APOL1-\u4ecb\u5bfc\u6027\u80be\u75c5\u7684\u521b\u65b0\u836finaxaplin\u3002\u6700\u8fd1\uff0c\u8be5\u516c\u53f8\u5ba3\u5e03\u542f\u52a8inaxaplin 2\/3\u671f\u4e34\u5e8a\u8bd5\u9a8c\u7684\u4e09\u671f\u3002\u8fd9\u4e00\u5019\u9009\u4ea7\u54c12a\u671f\u7684\u7ed3\u679c\u975e\u5e38\u4e0d\u9519\uff0c\u5176\u4e2d\u5305\u62ec\u86cb\u767d\u5c3f\u7edf\u8ba1\u4e0a\u7684\u663e\u8457\u4e0b\u964d\u3002\u57fa\u4e8e\u5230\u76ee\u524d\u4e3a\u6b62\u6240\u6536\u96c6\u7684\u6570\u636e\uff0c\u798f\u6cf0\u5236\u836f\u8ba1\u5212\u6269\u5927\u7814\u7a76\u8303\u56f4\uff0c\u5c0610\u5c81\u7684\u60a3\u8005\u4e5f\u7eb3\u5165\u5176\u4e2d\u3002<\/p>\n<p>\u76ee\u524dAPOL1-\u4ecb\u5bfc\u6027\u80be\u75c5\u5c1a\u65e0\u83b7\u6279\u836f\u7269\uff0c\u5e76\u4e14\u6309\u7167\u798f\u6cf0\u5236\u836f\u7684\u4f30\u7b97\uff0c\u7f8e\u56fd\u548c\u6b27\u6d32\u5c06\u670910\u4e07\u60a3\u8005\u53d7\u76ca\u4e8einaxaplin\u3002\u76f8\u6bd4\u4e4b\u4e0b\uff0c\u4e24\u5730\u7684\u56ca\u6027\u7ea4\u7ef4\u5316\u60a3\u8005\u4eba\u6570\u7ea6\u4e3a9.2\u4e07\u3002\u6362\u53e5\u8bdd\u8bf4\uff0c\u5982\u679cinaxaplin\u7684\u540e\u671f\u4e34\u5e8a\u8bd5\u9a8c\u53d6\u5f97\u6210\u529f\u5e76\u4e14\u6700\u7ec8\u83b7\u6279\u4e0a\u5e02\uff0c\u5b83\u7684\u5e02\u573a\u6f5c\u529b\u53ef\u6bd4\u8be5\u516c\u53f8\u7684CF\u4ea7\u54c1\u7ec4\u5408\u3002<\/p>\n<p>\u5c3d\u7ba1\u5982\u6b64\uff0c\u798f\u6cf0\u5236\u836f\u7684\u53d1\u5c55\u524d\u666f\u5e76\u4e0d\u5b8c\u5168\u4f9d\u8d56\u4e8einaxaplin\u8fd9\u4e00\u6b3e\u5019\u9009\u4ea7\u54c1\u3002\u5148\u4e0d\u8bf4\u540e\u671f\u7814\u7a76\u53ef\u80fd\u4f1a\u5931\u8d25\uff0c\u5c31\u7b97\u6210\u529f\uff0c\u4e5f\u4e0d\u80fd\u4fdd\u8bc1\u5176\u4ed6\u5236\u836f\u5546\u4e0d\u4f1a\u63d2\u4e00\u811a\uff0c\u4ece\u800c\u52a0\u5927\u5e02\u573a\u7684\u7ade\u4e89\u3002<\/p>\n<p>\u798f\u6cf0\u5236\u836f\u7684\u57fa\u672c\u9762\u548c\u6210\u957f\u6027\u90fd\u6ca1\u8bdd\u8bf4\u3002\u5f97\u76ca\u4e8e\u8be5\u516c\u53f8\u6700\u91cd\u8981\u7684\u4ea7\u54c1Trikafta\uff0c\u516c\u53f8\u53bb\u5e74\u7684\u9500\u552e\u989d\u540c\u6bd4\u589e\u957f11%\u81f398.7\u4ebf\u7f8e\u5143\uff0c\u6bcf\u80a1\u6536\u76ca\u589e\u957f8.3%\u81f313.89\u7f8e\u5143\u3002\u6b64\u5916\u5728\u53bb\u5e74\u5e74\u5e95\uff0c\u516c\u53f8\u8054\u5408CRISPR Therapeutics\u5f00\u53d1\u7684\u7f55\u89c1\u75c5\u57fa\u56e0\u7f16\u8f91\u7597\u6cd5Casgevy\u83b7\u5f97\u6279\u51c6\u3002\u6700\u540e\uff0c\u8be5\u516c\u53f8\u8fd8\u62a5\u544a\u4e86\u6cbb\u7597\u6025\u6027\u75db\u4ee5\u53caCF\u7684\u65b0\u7597\u6cd5\u79ef\u6781\u7684\u4e09\u671f\u7ed3\u679c\uff0c\u5e76\u4e14\u5b83\u4eec\u5747\u6709\u671b\u5728\u4e00\u5e74\u4e4b\u5185\u83b7\u5f97\u76d1\u7ba1\u673a\u6784\u7684\u6279\u51c6\u3002<\/p>\n<p>\u7b80\u5355\u6765\u8bf4\uff0c\u798f\u6cf0\u5236\u836f\u8fd9\u53ea\u6781\u5177\u521b\u65b0\u529b\u7684\u751f\u7269\u79d1\u6280\u80a1\u7968\u6709\u80fd\u529b\u6301\u7eed\u53d6\u5f97\u4e34\u5e8a\u548c\u76d1\u7ba1\u4e0a\u7684\u6210\u529f\uff0c\u6301\u7eed\u62ff\u51fa\u51fa\u8272\u7684\u4e1a\u7ee9\uff0c\u4ee5\u53ca\u8dd1\u8d62\u5e02\u573a\u7684\u56de\u62a5\u7387\u3002<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\u751f\u7269\u79d1\u6280\u5de8\u5934\u798f\u6cf0\u5236\u836fVertex Pharmaceuticals\uff08NASDAQ:VRTX\uff09\u5c31\u662f\u4e00\u53f0\u4e0d\u65ad\u5411\u524d\u7684\u521b [&hellip;]<\/p>\n","protected":false},"author":27,"featured_media":493764,"comment_status":"closed","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"footnotes":"","_links_to":"","_links_to_target":""},"categories":[1521,430],"tags":[455,747,2155,925],"class_list":["post-493763","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-1521","category-trends-strategies-zh-hans","tag-455","tag-747","tag-2155","tag-925","sectors-life-science-zh-hans","locations-us-zh-hans","exchange-nasdaq-zh-hans"],"acf":[],"_links":{"self":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts\/493763","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/users\/27"}],"replies":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/comments?post=493763"}],"version-history":[{"count":1,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts\/493763\/revisions"}],"predecessor-version":[{"id":493771,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts\/493763\/revisions\/493771"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/media\/493764"}],"wp:attachment":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/media?parent=493763"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/categories?post=493763"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/tags?post=493763"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}