{"id":616469,"date":"2026-01-21T23:44:25","date_gmt":"2026-01-22T07:44:25","guid":{"rendered":"https:\/\/nai500.com\/?p=616469"},"modified":"2026-01-21T23:44:25","modified_gmt":"2026-01-22T07:44:25","slug":"%e8%a7%a3%e7%a0%81%e5%9f%ba%e5%9b%a0%e7%bc%96%e8%be%91%e8%b5%9b%e9%81%93%e5%85%b3%e6%b3%a8%e4%b8%89%e5%a4%a7%e9%a2%86%e5%85%88%e4%bc%81%e4%b8%9a%e8%bf%9b%e5%b1%95%e4%b8%8e%e6%8a%95%e8%b5%84%e8%a7%86","status":"publish","type":"post","link":"https:\/\/nai500.com\/zh-hans\/blog\/2026\/01\/%e8%a7%a3%e7%a0%81%e5%9f%ba%e5%9b%a0%e7%bc%96%e8%be%91%e8%b5%9b%e9%81%93%e5%85%b3%e6%b3%a8%e4%b8%89%e5%a4%a7%e9%a2%86%e5%85%88%e4%bc%81%e4%b8%9a%e8%bf%9b%e5%b1%95%e4%b8%8e%e6%8a%95%e8%b5%84%e8%a7%86\/","title":{"rendered":"\u89e3\u7801\u57fa\u56e0\u7f16\u8f91\u8d5b\u9053\uff0c\u5173\u6ce8\u4e09\u5927\u9886\u5148\u4f01\u4e1a\u8fdb\u5c55\u4e0e\u6295\u8d44\u89c6\u89d2"},"content":{"rendered":"<p class=\"p1\"><span class=\"s1\">\u57fa\u56e0\u7f16\u8f91\u6280\u672f\u901a\u8fc7\u76f4\u63a5\u4fee\u6539DNA\uff0c\u4e3a\u6cbb\u7597\u4e43\u81f3\u6cbb\u6108\u7531\u57fa\u56e0\u53d8\u5f02\u5f15\u8d77\u7684\u75be\u75c5\u63d0\u4f9b\u4e86\u9769\u547d\u6027\u6f5c\u529b\u3002\u636e\u9884\u6d4b\uff0c\u52302032\u5e74\uff0c\u5168\u7403\u57fa\u56e0\u7f16\u8f91\u5e02\u573a\u89c4\u6a21\u6709\u671b\u8fbe\u5230308\u4ebf\u7f8e\u5143\u3002\u5728\u8fd9\u4e00\u5145\u6ee1\u524d\u666f\u7684\u8d5b\u9053\u4e2d\uff0c\u6570\u5bb6\u9886\u5148\u7684\u751f\u7269\u6280\u672f\u516c\u53f8\u6b63\u63a8\u52a8\u7597\u6cd5\u8d70\u5411\u5e02\u573a\uff0c\u5438\u5f15\u4e86\u6295\u8d44\u8005\u7684\u9ad8\u5ea6\u5173\u6ce8\u3002<\/span><\/p>\n<h2 class=\"p1\"><span class=\"s1\">Intellia Therapeutics\uff1a\u6df1\u8015\u4f53\u5185\u7f16\u8f91\u7597\u6cd5<\/span><\/h2>\n<p class=\"p1\"><span class=\"s1\">\u7531Jennifer Doudna\u4e8e2014\u5e74\u8054\u5408\u521b\u7acb\u7684<a href=\"https:\/\/nai500.com\/zh-hans\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%af%a2\/?qm_symbol=ntla\"><span class=\"s2\">Intellia Therapeutics\uff08NTLA\uff09<\/span><\/a>\uff0c\u81f4\u529b\u4e8e\u5f00\u53d1\u5177\u6709\u6f5c\u5728\u6cbb\u6108\u4f5c\u7528\u7684\u57fa\u56e0\u7f16\u8f91\u7597\u6cd5\u30022021\u5e74\uff0c\u8be5\u516c\u53f8\u4e0e\u5408\u4f5c\u4f19\u4f34<a href=\"https:\/\/nai500.com\/zh-hans\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%af%a2\/?qm_symbol=regn\"><span class=\"s2\">Regeneron Pharmaceuticals\uff08REGN\uff09<\/span><\/a>\u516c\u5e03\u4e86\u9996\u4e2a\u652f\u6301\u5728\u4eba\u4f53\u5185\u4f7f\u7528CRISPR-Cas9\u57fa\u56e0\u7f16\u8f91\u7684\u4e34\u5e8a\u6570\u636e\uff0c\u6807\u5fd7\u7740\u91cd\u8981\u91cc\u7a0b\u7891\u3002\u76ee\u524d\uff0c\u53cc\u65b9\u6b63\u5408\u4f5c\u5f00\u5c55\u9488\u5bf9\u8f6c\u7532\u72b6\u817a\u7d20\u86cb\u767d\u6dc0\u7c89\u6837\u53d8\u6027\uff08ATTR\uff09\u7684\u540e\u671f\u7814\u7a76\uff0c\u8bc4\u4f30\u836f\u7269nexiguran ziclumeran\uff08\u539f\u540dNTLA-2001\uff09\u3002\u6b64\u5916\uff0cIntellia\u5168\u8d44\u62e5\u6709\u7684\u540e\u671f\u5019\u9009\u836f\u7269NTLA-2002\uff0c\u8ba1\u5212\u4e8e2026\u5e74\u4e0b\u534a\u5e74\u5411\u7f8e\u56fd\u76d1\u7ba1\u673a\u6784\u63d0\u4ea4\u7533\u8bf7\uff0c\u7528\u4e8e\u6cbb\u7597\u9057\u4f20\u6027\u8840\u7ba1\u6027\u6c34\u80bf\uff08HAE\uff09\u3002\u82e5\u5176\u6388\u6743\u7ed9\u518d\u751f\u5143\u516c\u53f8\u7684B\u578b\u8840\u53cb\u75c5\u7597\u6cd5\u540e\u7eed\u8fdb\u5c55\u987a\u5229\uff0cIntellia\u8fd8\u5c06\u6709\u8d44\u683c\u83b7\u5f97\u91cc\u7a0b\u7891\u4ed8\u6b3e\u548c\u7279\u8bb8\u6743\u4f7f\u7528\u8d39\u3002<\/span><\/p>\n<h2 class=\"p1\"><span class=\"s1\">CRISPR Therapeutics\uff1a\u4ece\u9996\u6b3e\u83b7\u6279\u5230\u7ba1\u7ebf\u62d3\u5c55<\/span><\/h2>\n<p class=\"p1\"><span class=\"s2\"><a href=\"https:\/\/nai500.com\/zh-hans\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%af%a2\/?qm_symbol=crsp\">CRISPR Therapeutics\uff08CRSP\uff09<\/a><\/span><span class=\"s1\">\u7531Emmanuelle Charpentier\u4e8e2013\u5e74\u8054\u5408\u521b\u7acb\u3002\u8be5\u516c\u53f8\u4e0e<a href=\"https:\/\/nai500.com\/zh-hans\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%af%a2\/?qm_symbol=vrtx\"><span class=\"s2\">Vertex Pharmaceuticals\uff08VRTX\uff09<\/span><\/a>\u5408\u4f5c\u7684\u57fa\u56e0\u7f16\u8f91\u7597\u6cd5Casgevy\uff0c\u4e8e2023\u5e7412\u6708\u7387\u5148\u83b7\u5f97\u76d1\u7ba1\u6279\u51c6\uff0c\u7528\u4e8e\u6cbb\u7597\u9570\u72b6\u7ec6\u80de\u8d2b\u8840\u75c7\uff0c\u968f\u540e\u53c8\u83b7\u6279\u7528\u4e8e\u6cbb\u7597\u8f93\u8840\u4f9d\u8d56\u578b\u03b2-\u5730\u4e2d\u6d77\u8d2b\u8840\u75c7\uff0c\u5b9e\u73b0\u4e86\u8be5\u9886\u57df\u7684\u5546\u4e1a\u5316\u7a81\u7834\u3002\u5728Casgevy\u5546\u4e1a\u5316\u6301\u7eed\u63a8\u8fdb\u7684\u540c\u65f6\uff0c\u516c\u53f8\u7814\u53d1\u7ba1\u7ebf\u6db5\u76d6\u591a\u9879\u521b\u65b0\u9879\u76ee\uff0c\u5305\u62ec\u6b63\u5728\u8fdb\u884c\u4e34\u5e8a\u8bd5\u9a8c\u7684\u4e24\u79cd\u540c\u79cd\u5f02\u4f53CAR-T\u7597\u6cd5CTX112\u548cCTX131\uff0c\u4ee5\u53ca\u4e24\u79cd\u5904\u4e8e\u65e9\u671f\u4e34\u5e8a\u7814\u7a76\u7684\u4f53\u5185\u57fa\u56e0\u7f16\u8f91\u7597\u6cd5\u548c\u4e00\u9879\u6cbb\u75971\u578b\u7cd6\u5c3f\u75c5\u7684\u5b9e\u9a8c\u6027\u7597\u6cd5\u3002<\/span><\/p>\n<h2 class=\"p1\"><span class=\"s1\">Beam Therapeutics\uff1a\u63a2\u7d22\u7cbe\u51c6\u78b1\u57fa\u7f16\u8f91<\/span><\/h2>\n<p class=\"p1\"><span class=\"s2\"><a href=\"https:\/\/nai500.com\/zh-hans\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%af%a2\/?qm_symbol=beam\">Beam Therapeutics\uff08BEAM\uff09<\/a><\/span><span class=\"s1\">\u7531David Liu\u548cFeng Zhang\u4e8e2017\u5e74\u8054\u5408\u521b\u7acb\uff0c\u4e13\u6ce8\u4e8e\u78b1\u57fa\u7f16\u8f91\u6280\u672f\u30022025\u5e743\u6708\uff0c\u8be5\u516c\u53f8\u516c\u5e03\u4e86BEAM-302\u6cbb\u7597\u03b1-1\u6297\u80f0\u86cb\u767d\u9176\u7f3a\u4e4f\u75c7\uff08AATD\uff09\u7684I\/II\u671f\u4e34\u5e8a\u7814\u7a76\u7684\u79ef\u6781\u521d\u6b65\u7ed3\u679c\u3002\u540c\u65f6\uff0c\u5176\u9488\u5bf9\u9570\u72b6\u7ec6\u80de\u8d2b\u8840\u75c7\u7684\u5019\u9009\u836f\u7269risto-cel\uff08\u539f\u540dBEAM-101\uff09\u7684I\/II\u671f\u4e34\u5e8a\u7814\u7a76\u4e5f\u5728\u8fdb\u884c\u4e2d\uff0c\u5e76\u8ba1\u5212\u6700\u65e9\u4e8e2026\u5e74\u5e95\u63d0\u4ea4\u4e0a\u5e02\u7533\u8bf7\u3002\u6b64\u5916\uff0c\u516c\u53f8\u9884\u8ba1\u57282026\u5e74\u516c\u5e03BEAM-301\u6cbb\u7597\u7cd6\u539f\u8d2e\u79ef\u75c71a\u4ee5\u53caBEAM-302\u6cbb\u7597AATD\u7684\u66f4\u591a\u4e34\u5e8a\u8bd5\u9a8c\u6570\u636e\u3002<\/span><\/p>\n<h2 class=\"p1\"><span class=\"s1\">\u6295\u8d44\u98ce\u9669\u4e0e\u6311\u6218\u4e0d\u5bb9\u5ffd\u89c6<\/span><\/h2>\n<p class=\"p1\"><span class=\"s1\">\u5c3d\u7ba1\u57fa\u56e0\u7f16\u8f91\u9886\u57df\u957f\u671f\u56de\u62a5\u6f5c\u529b\u53ef\u89c2\uff0c\u4f46\u6295\u8d44\u76f8\u5173\u80a1\u7968\u4e5f\u4f34\u968f\u7740\u663e\u8457\u98ce\u9669\u3002\u8fd9\u4e9b\u98ce\u9669\u5305\u62ec\u80a1\u4ef7\u7684\u9ad8\u6ce2\u52a8\u6027\u3001\u516c\u53f8\u56e0\u8d44\u672c\u9700\u6c42\u53ef\u80fd\u5bfc\u81f4\u73b0\u6709\u80a1\u7968\u4ef7\u503c\u88ab\u7a00\u91ca\u3001\u4e34\u5e8a\u8bd5\u9a8c\u5931\u8d25\u7684\u53ef\u80fd\u6027\u3001\u672a\u80fd\u83b7\u5f97\u76d1\u7ba1\u90e8\u95e8\u6279\u51c6\u7684\u98ce\u9669\uff0c\u4ee5\u53ca\u7597\u6cd5\u83b7\u6279\u540e\u53ef\u80fd\u9762\u4e34\u7684\u62a5\u9500\u969c\u788d\u3002<\/span><\/p>\n","protected":false},"excerpt":{"rendered":"<p>\u57fa\u56e0\u7f16\u8f91\u6280\u672f\u901a\u8fc7\u76f4\u63a5\u4fee\u6539DNA\uff0c\u4e3a\u6cbb\u7597\u4e43\u81f3\u6cbb\u6108\u7531\u57fa\u56e0\u53d8\u5f02\u5f15\u8d77\u7684\u75be\u75c5\u63d0\u4f9b\u4e86\u9769\u547d\u6027\u6f5c\u529b\u3002\u636e\u9884\u6d4b\uff0c\u52302032\u5e74\uff0c\u5168\u7403 [&hellip;]<\/p>\n","protected":false},"author":9,"featured_media":598764,"comment_status":"closed","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"footnotes":"","_links_to":"","_links_to_target":""},"categories":[427],"tags":[820,455,747,925],"class_list":["post-616469","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-market-news-zh-hans","tag-820","tag-455","tag-747","tag-925","sectors-life-science-zh-hans","locations-us-zh-hans","exchange-nasdaq-zh-hans","exchange-nyse-zh-hans"],"acf":[],"_links":{"self":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts\/616469","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/users\/9"}],"replies":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/comments?post=616469"}],"version-history":[{"count":3,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts\/616469\/revisions"}],"predecessor-version":[{"id":616472,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/posts\/616469\/revisions\/616472"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/media\/598764"}],"wp:attachment":[{"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/media?parent=616469"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/categories?post=616469"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/nai500.com\/zh-hans\/wp-json\/wp\/v2\/tags?post=616469"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}