{"id":242926,"date":"2018-10-20T00:01:14","date_gmt":"2018-10-20T07:01:14","guid":{"rendered":"https:\/\/nai500.com\/?p=242926"},"modified":"2018-10-20T00:01:14","modified_gmt":"2018-10-20T07:01:14","slug":"%e5%9f%ba%e5%9b%a0%e6%b2%bb%e7%99%82%e3%80%81%e5%9f%ba%e5%9b%a0%e7%b7%a8%e8%bc%af%e5%92%8c%e5%85%8d%e7%96%ab%e8%85%ab%e7%98%a4%e5%ad%b8%e5%89%b5%e9%80%a0%e4%ba%86%e6%95%b8%e5%8d%83%e5%80%8b%e6%96%b0","status":"publish","type":"post","link":"https:\/\/nai500.com\/zh-hant\/blog\/2018\/10\/%e5%9f%ba%e5%9b%a0%e6%b2%bb%e7%99%82%e3%80%81%e5%9f%ba%e5%9b%a0%e7%b7%a8%e8%bc%af%e5%92%8c%e5%85%8d%e7%96%ab%e8%85%ab%e7%98%a4%e5%ad%b8%e5%89%b5%e9%80%a0%e4%ba%86%e6%95%b8%e5%8d%83%e5%80%8b%e6%96%b0\/","title":{"rendered":"\u57fa\u56e0\u6cbb\u7642\u3001\u57fa\u56e0\u7de8\u8f2f\u548c\u514d\u75ab\u816b\u7624\u5b78\u5275\u9020\u4e86\u6578\u5343\u500b\u65b0\u7684\u5c31\u696d\u6a5f\u6703"},"content":{"rendered":"

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Sangamo Therapeutics\u7e3d\u90e8\u4f4d\u65bc\u52a0\u5229\u798f\u5c3c\u4e9e\u5dde\uff0c\u662f\u4e00\u5bb6\u5c08\u8a3b\u65bc\u57fa\u56e0\u6cbb\u7642\u548c\u57fa\u56e0\u7d44\u7de8\u8f2f\u7684\u516c\u53f8\u3002 9\u6708\uff0c\u8a72\u516c\u53f8\u5ba3\u5e03\u6210\u529f\u9032\u884cSB-913\u7684I \/ II\u671f\u81e8\u5e8a\u8a66\u9a57\u3002SB-913\u662f\u4e00\u7a2e\u92c5\u6307\u6838\u9178\u9176\u9ad4\u5167\u57fa\u56e0\u7d44\u7de8\u8f2f\u7522\u54c1\uff0c\u65e8\u5728\u6cbb\u7642MPS II\uff0c\u4e5f\u7a31\u70ba\u4ea8\u7279\u7d9c\u5408\u5f81\u3002\u82f1\u570b\u5ee3\u64ad\u516c\u53f8\u6700\u8fd1\u5831\u9053\u4e86\u9019\u4e00\u8da8\u52e2\uff0c\u5c0d\u63a5\u53d7\u5be6\u9a57\u6027\u6cbb\u7642\u7684\u60a3\u8005\u9032\u884c\u4e86\u63cf\u8ff0\u3002 Sangamo\u7684\u9996\u5e2d\u57f7\u884c\u5b98Sandy Macrae\u544a\u8a34BBC\uff1a\u201c\u6211\u5011\u6b63\u8655\u65bc\u57fa\u56e0\u7d44\u91ab\u5b78\u65b0\u9818\u57df\u7684\u524d\u7aef\u3002\u201d<\/p>\n

BioSpace\u6700\u8fd1\u5728\u5b98\u7db2\u4e0a\u9032\u884c\u4e86\u4e00\u9805\u7c21\u77ed\u8abf\u67e5\uff0c\u8a62\u554f\u4eba\u5011\u770b\u5230\u7684\u8da8\u52e2\u3002\u5176\u4e2d\u4e00\u500b\u8da8\u52e2\u662f\u57fa\u56e0\u6cbb\u7642\uff0c\u5be6\u4f8b\u5305\u62ecBioMarin Pharmaceutical\uff0c\u8a72\u516c\u53f8\u65bc2017\u5e748\u6708\u5728\u52a0\u5229\u798f\u5c3c\u4e9e\u5dde\u958b\u8a2d\u4e86\u4e00\u5bb6\u65b0\u7684\u751f\u7522\u5de5\u5ee0\uff0c\u751f\u7522\u6cbb\u7642\u56b4\u91cd\u8840\u53cb\u75c5\u7684\u85e5\u7269BMN 270\u3002<\/p>\n

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\u9810\u8a082017\u5e74\u5168\u7403\u57fa\u56e0\u7d44\u7de8\u8f2f\u5e02\u5834\u898f\u6a21\u5c07\u7ffb\u4e00\u756a\uff0c\u9054\u523062.8\u5104\u7f8e\u5143\u3002\u82f1\u570b\u653f\u5e9c\u5ba3\u5e03\u5c07\u5411\u65b0\u7684\u7d30\u80de\u548c\u57fa\u56e0\u6cbb\u7642\u5236\u9020\u4e2d\u5fc3\u6295\u5165\u76f8\u7576\u65bc7600\u842c\u7f8e\u5143\u7684\u8cc7\u91d1\u3002\u5728\u7f8e\u570b\uff0c\u570b\u5bb6\u4eba\u985e\u57fa\u56e0\u7d44\u7814\u7a76\u6240\u9810\u8a08\u5d17\u4f4d\u5c07\u201c\u5927\u5e45\u589e\u52a0\u201d\u3002<\/p>\n

\u82f1\u6587\u4f86\u6e90\uff1a Biospace<\/p>\n","protected":false},"excerpt":{"rendered":"

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