{"id":473019,"date":"2023-09-24T19:10:44","date_gmt":"2023-09-25T02:10:44","guid":{"rendered":"https:\/\/nai500.com\/blog\/2023\/09\/%e5%9f%ba%e5%9b%a0%e7%bc%96%e8%be%91%e8%82%a1%e7%a5%a8-%e4%ba%8c%e9%80%89%e4%b8%80-intellia-rocket\/"},"modified":"2023-09-24T19:11:09","modified_gmt":"2023-09-25T02:11:09","slug":"%e5%9f%ba%e5%9b%a0%e7%b7%a8%e8%bc%af%e8%82%a1%e7%a5%a8-%e4%ba%8c%e9%81%b8%e4%b8%80-intellia-rocket","status":"publish","type":"post","link":"https:\/\/nai500.com\/zh-hant\/blog\/2023\/09\/%e5%9f%ba%e5%9b%a0%e7%b7%a8%e8%bc%af%e8%82%a1%e7%a5%a8-%e4%ba%8c%e9%81%b8%e4%b8%80-intellia-rocket\/","title":{"rendered":"\u57fa\u56e0\u7de8\u8f2f\u80a1\u7968\u4e8c\u9078\u4e00\uff1aIntellia Therapeutics\u9084\u662fRocket Pharmaceuticals"},"content":{"rendered":"<h2>Rocket\u7684\u85e5\u54c1\u66f4\u5feb\u4e0a\u5e02\uff0c\u4f46Intellia\u7684\u76ee\u6a19\u5e02\u5834\u66f4\u5927<\/h2>\n<p><a href=\"https:\/\/nai500.com\/zh-hans\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%af%a2\/?qm_symbol=RCKT\">Rocket Pharmaceuticals Inc\uff08NASDAQ:RCKT\uff09<\/a>\u548cRocket Pharmaceuticals Inc\uff08NASDAQ:RCKT\uff09\u9019\u5169\u96bb\u57fa\u56e0\u7de8\u8f2f\u751f\u7269\u79d1\u6280\u516c\u53f8\u90fd\u81f4\u529b\u65bc\u958b\u767c\u76ee\u524d\u91ab\u85e5\u79d1\u5b78\u5c1a\u7121\u6cd5\u6cbb\u7652\u7684\u907a\u50b3\u6027\u75be\u75c5\u7684\u7642\u6cd5\uff0c\u4f46\u9019\u5169\u5bb6\u516c\u53f8\u76ee\u524d\u4ecd\u8655\u65bc\u81e8\u5e8a\u8a66\u9a57\u968e\u6bb5\uff0c\u6536\u5165\u5168\u90e8\u4f86\u81ea\u65bc\u8ddf\u5176\u4ed6\u88fd\u85e5\u516c\u53f8\u7684\u5408\u4f5c\u3002<\/p>\n<p>\u9019\u5169\u96bb\u57fa\u56e0\u7de8\u8f2f\u80a1\u7968\u8ab0\u7684\u6210\u529f\u5e7e\u7387\u66f4\u5927\uff1f\u6211\u5011\u8a66\u8457\u5f9e\u7814\u767c\u7ba1\u7dda\u6210\u719f\u5ea6\uff0c\u73fe\u91d1\u6301\u6709\u91cf\u4ee5\u53ca\u76ee\u6a19\u5e02\u5834\u7684\u898f\u6a21\u9032\u884c\u4e00\u500b\u5206\u6790\u3002<\/p>\n<h2>Rocket\u5373\u5c07\u5728\u591a\u500b\u7f55\u898b\u75c5\u5e02\u5834\u4e0a\u7206\u767c<\/h2>\n<p>Rocket Pharmaceuticals\u5373\u5c07\u5728\u591a\u500b\u76ee\u524d\u5c1a\u7121\u6cbb\u7642\u65b9\u6848\u7684\u7f55\u898b\u75c5\u5e02\u5834\u4e0a\u63a8\u51fa\u7b2c\u4e00\u6b3e\u85e5\u7269\u3002<\/p>\n<p>\u5177\u9ad4\u4f86\u770b\uff0c\u6cbb\u7652\u6216\u6cbb\u7642\u81f4\u6b7b\u6027\u907a\u50b3\u5fc3\u81df\u75c5Danon\u75c5\uff08\u7f8e\u570b\u548c\u6b50\u6d32\u60a3\u8005\u4eba\u6578\u6700\u9ad83\u842c\uff09\u7684\u5019\u9078\u7522\u54c1\u5373\u5c07\u9032\u5165\u4e8c\u671f\u81e8\u5e8a\u8a66\u9a57\u3002Fanconi\u8ca7\u8840\uff08\u6bcf\u5e74\u9810\u8a08\u60a3\u8005\u4eba\u6578\u6700\u9ad8275\u4eba\uff09\u7684\u7814\u767c\u9805\u76ee\u9810\u8a08\u5c07\u5728\u672a\u4f86\u5e7e\u500b\u5b63\u5ea6\u5be6\u73fe\u7533\u8acb\u7684\u63d0\u4ea4\u548c\u5546\u696d\u5316\u3002\u6b64\u5916\uff0c\u516c\u53f8\u5df2\u7d93\u5411\u7f8e\u570b\u98df\u54c1\u85e5\u54c1\u76e3\u7ba1\u5c40\uff08FDA\uff09\u63d0\u4ea4\u4e86\u6cbb\u7642\u56b4\u91cdI\u578b\u767d\u7d30\u80de\u7c98\u9644\u7f3a\u9677\uff08LAD-I\uff0c\u6bcf\u5e74\u7f8e\u570b\u548c\u6b50\u6d32\u7684\u60a3\u8005\u4eba\u6578\u572850\u81f375\u4eba\u4e4b\u9593\uff09\u7684\u5019\u9078\u7522\u54c1\u7684\u4e0a\u5e02\u7533\u8acb\u3002<\/p>\n<p>\u9452\u65bc\u8a72\u516c\u53f8\u525b\u525b\u767c\u884c\u4e861.75\u5104\u7f8e\u5143\u7684\u65b0\u80a1\u548c\u9810\u7c4c\u8cc7\u8a8d\u80a1\u6b0a\u8b49\uff0c\u540c\u6642\u622a\u81f3\u4e8c\u5b63\u5ea6\u7684\u73fe\u91d1\u53ca\u73fe\u91d1\u7b49\u50f9\u7269\u70ba3.07\u5104\u7f8e\u5143\uff0c\u9019\u4e9b\u8cc7\u91d1\u53ef\u4ee5\u652f\u6490\u5b83\u4e0d\u5230\u5169\u5e74\u7684\u7d93\u71df\u3002\u5982\u679cRocket\u7684\u5169\u500b\u7814\u767c\u9805\u76ee\u81f3\u5c11\u6709\u4e00\u500b\u6210\u529f\u5be6\u73fe\u5546\u696d\u5316\uff0c\u516c\u53f8\u6709\u671b\u57282024\u5e74\u5e95\u4e4b\u524d\u76c8\u5229\u3002\u4f46\u662f\uff0c\u7531\u65bc\u8a72\u516c\u53f8\u7684\u76ee\u6a19\u5e02\u5834\u5be6\u5728\u662f\u592a\u5c0f\uff0c\u52a0\u4e0a\u5b83\u7684\u57fa\u56e0\u7de8\u8f2f\u7642\u6cd5\u50c5\u9700\u4e00\u5291\u5c31\u80fd\u63d0\u4f9b\u9577\u671f\u7684\u7642\u6548\u751a\u81f3\u662f\u6c38\u4e45\u6cbb\u7652\uff0c\u516c\u53f8\u7684\u9577\u4e45\u751f\u5b58\u59cb\u7d42\u662f\u4e00\u500b\u98a8\u96aa\u3002<\/p>\n<h2>Intellia\u7684\u76c8\u5229\u9053\u8def\u66f4\u9577\uff0c\u4f46\u66f4\u6709\u201c\u9322\u666f\u201d<\/h2>\n<p>\u76f8\u6bd4Rocket Pharmaceuticals\uff0cIntellia Therapeutics\u7684\u5728\u7814\u7ba1\u7dda\u6210\u719f\u5ea6\u4e0d\u53ca\u524d\u8005\uff0c\u516c\u53f8\u7684\u5169\u500b\u81e8\u5e8a\u9805\u76ee\u8ddd\u96e2\u5546\u696d\u5316\u9084\u5f88\u9059\u9060\u3002\u9019\u5169\u500b\u7814\u767c\u9805\u76ee\u5206\u5225\u6cbb\u7642\u7684\u662f\u8f49\u7532\u72c0\u817a\u7d20\u86cb\u767d\uff08ATTR\uff0c\u4e00\u7a2e\u5168\u7403\u60a3\u8005\u4eba\u6578\u6700\u9ad850\u842c\u7684\u81f4\u6b7b\u6027\u57fa\u56e0\u75be\u75c5\uff09\uff0c\u4ee5\u53ca\u907a\u50b3\u6027\u8840\u7ba1\u6027\u6c34\u816b\uff08HAE\uff0c\u907a\u50b3\u6027\u75be\u75c5\uff0c\u5168\u7403\u60a3\u8005\u4eba\u6578\u7d0416.2\u842c\uff0c\u767c\u75c5\u7387\u70ba5\u842c\u5206\u4e4b\u4e00\uff09\u3002<\/p>\n<p>\u6309\u7167\u7ba1\u7406\u5c64\u7684\u4f30\u7b97\uff0cATTR\u6cbb\u7642\u7684\u5e02\u5834\u898f\u6a21\u52302026\u5e74\u6216\u63a5\u8fd1120\u5104\u7f8e\u5143\uff0c\u540c\u6642HAE\u85e5\u7269\u7684\u6f5b\u5728\u5e02\u5834\u898f\u6a21\u70ba40\u5104\u7f8e\u5143\u3002\u96d6\u7136\u90fd\u662f\u7f55\u898b\u75c5\uff0c\u4f46Intellia\u7684\u76ee\u6a19\u5e02\u5834\u660e\u986f\u5927\u65bcRocket\uff0c\u56e0\u6b64\u5b83\u7684\u6536\u5165\u6f5b\u529b\u548c\u6301\u7e8c\u6027\u90fd\u8981\u66f4\u512a\u3002\u63db\u53e5\u8a71\u8aaa\uff0c\u9019\u5169\u96bb\u57fa\u56e0\u7de8\u8f2f\u80a1\u7968\u7684\u81e8\u5e8a\u7814\u7a76\u6216\u5be9\u6279\u98a8\u96aa\u5dee\u5225\u4e0d\u5927\uff0c\u4f46Intellia\u5728\u85e5\u54c1\u5546\u696d\u5316\u4e4b\u5f8c\u7684\u8ca1\u52d9\u98a8\u96aa\u8981\u5c0f\u5f97\u591a\u3002<\/p>\n<p>Intellia\u904e\u53bb12\u500b\u6708\u7684\u7d93\u71df\u6210\u672c\u70ba5.13\u5104\u7f8e\u5143\uff0c\u800c\u73fe\u91d1\u3001\u73fe\u91d1\u7b49\u50f9\u7269\u4ee5\u53ca\u77ed\u671f\u6295\u8cc7\u90549.08\u5104\u7f8e\u5143\u3002\u96d6\u7136\u9810\u7b97\u66f4\u9ad8\uff0c\u4f46\u73fe\u91d1\u7684\u71d2\u9322\u6301\u7e8c\u6642\u9577\u985e\u4f3c\u3002<\/p>\n<p>\u77ed\u671f\u4f86\u770b\uff0cRocket Pharmaceuticals\u7684\u80a1\u50f9\u51fa\u73fe\u66f4\u5feb\u4e0a\u6f32\u5c07\u662f\u5927\u6982\u7387\u4e8b\u4ef6\uff0c\u5169\u6b3e\u85e5\u7269\u7372\u6279\u4ee5\u53ca\u85e5\u54c1\u92b7\u552e\u5e36\u4f86\u7684\u6536\u5165\u5c07\u5728\u5e02\u5834\u4e0a\u7372\u5f97\u7a4d\u6975\u7684\u53cd\u6620\u3002\u4e0d\u904e\u9577\u671f\u4f86\u770b\uff0c\u8a72\u516c\u53f8\u5927\u6982\u7387\u4e5f\u5c07\u89f8\u53ca\u589e\u9577\u7684\u5929\u82b1\u677f\uff0c\u751a\u81f3\u53ef\u80fd\u81ea\u5df1\u628a\u81ea\u5df1\u6dd8\u6c70\u51fa\u5e02\u5834\u3002\u7d50\u8ad6\u5c31\u662f\uff0cRocket\u4e0d\u662f\u4e00\u96bb\u5dee\u7684\u80a1\u7968\uff0c\u4f46\u8981\u8ad6\u8ab0\u624d\u662f\u66f4\u597d\u7684\u57fa\u56e0\u7de8\u8f2f\u751f\u7269\u79d1\u6280\u80a1\uff0cIntellia\u66f4\u52dd\u4e00\u7c4c\u3002<\/p>\n","protected":false},"excerpt":{"rendered":"<p>Rocket\u7684\u85e5\u54c1\u66f4\u5feb\u4e0a\u5e02\uff0c\u4f46Intellia\u7684\u76ee\u6a19\u5e02\u5834\u66f4\u5927 Rocket Pharmaceuticals I [&hellip;]<\/p>\n","protected":false},"author":27,"featured_media":443498,"comment_status":"closed","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"footnotes":"","_links_to":"","_links_to_target":""},"categories":[1522,431],"tags":[1788,809,927,564],"class_list":["post-473019","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-1522","category-trends-strategies-zh-hant","tag-1788","tag-809","tag-927","tag-564","sectors-life-science-zh-hant","locations-us-zh-hant","exchange-nasdaq-zh-hant"],"acf":[],"_links":{"self":[{"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/posts\/473019","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/users\/27"}],"replies":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/comments?post=473019"}],"version-history":[{"count":0,"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/posts\/473019\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/media\/443498"}],"wp:attachment":[{"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/media?parent=473019"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/categories?post=473019"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/tags?post=473019"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}