{"id":478974,"date":"2023-11-24T00:18:06","date_gmt":"2023-11-24T08:18:06","guid":{"rendered":"https:\/\/nai500.com\/blog\/2023\/11\/%e8%bf%99%e5%8f%aa%e6%88%90%e9%95%bf%e8%82%a1%e6%9a%b4%e6%b6%a8%e5%88%86%e6%9e%90%e5%b8%88%e8%ae%a4%e4%b8%ba%e8%bf%98%e5%8f%af%e4%bb%a5%e6%9b%b4%e9%ab%98\/"},"modified":"2023-11-24T00:24:45","modified_gmt":"2023-11-24T08:24:45","slug":"%e9%80%99%e5%8f%aa%e6%88%90%e9%95%b7%e8%82%a1%e6%9a%b4%e6%bc%b2%e5%88%86%e6%9e%90%e5%b8%ab%e8%aa%8d%e7%82%ba%e9%82%84%e5%8f%af%e4%bb%a5%e6%9b%b4%e9%ab%98","status":"publish","type":"post","link":"https:\/\/nai500.com\/zh-hant\/blog\/2023\/11\/%e9%80%99%e5%8f%aa%e6%88%90%e9%95%b7%e8%82%a1%e6%9a%b4%e6%bc%b2%e5%88%86%e6%9e%90%e5%b8%ab%e8%aa%8d%e7%82%ba%e9%82%84%e5%8f%af%e4%bb%a5%e6%9b%b4%e9%ab%98\/","title":{"rendered":"\u9019\u53ea\u6210\u9577\u80a1\u66b4\u6f3277%\uff01\u5206\u6790\u5e2b\u8a8d\u70ba\u9084\u53ef\u4ee5\u66f4\u9ad8"},"content":{"rendered":"<p>11\u670816\u65e5\uff0c\u82f1\u570b\u85e5\u54c1\u76e3\u7ba1\u6a5f\u69cb\u6279\u51c6\u4e86\u4e00\u7a2e\u4f7f\u7528CRISPR-Cas9\u57fa\u56e0\u7de8\u8f2f\u5de5\u5177\u7684\u7642\u6cd5\u3002\u9019\u4f7f\u6210\u9577\u80a1<a href=\"https:\/\/nai500.com\/zh-hant\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%a9%a2\/?qm_symbol=CRSP\">CRISPR Therapeutics\uff08CRSP\uff09<\/a>\u958b\u555f\u8d85\u901f\u904b\u8f49\u6a21\u5f0f\u3002\u9019\u7a2e\u7642\u6cd5\u662f\u7531\u4f4d\u65bc\u745e\u58eb\u7684\u751f\u7269\u79d1\u6280\u516c\u53f8CRISPR Therapeutics\u8207\u99ac\u85a9\u8af8\u585e\u5dde\u6ce2\u58eb\u9813\u7684<a href=\"https:\/\/nai500.com\/zh-hant\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%a9%a2\/?qm_symbol=VRTX\">Vertex Pharmaceuticals<\/a>\u5408\u4f5c\u958b\u767c\u7684\u3002\u5728\u82f1\u570b\u6210\u70ba\u7b2c\u4e00\u500b\u6279\u51c6\u57fa\u56e0\u7de8\u8f2f\u7642\u6cd5\u7684\u570b\u5bb6\u5f8c\uff0c\u6210\u9577\u80a1CRISPR Therapeutics\u7684\u80a1\u50f9\u5728\u904e\u53bb\u4e00\u500b\u6708\u88e1\u98c6\u5347\u3002\u63a5\u4e0b\u4f86\u662f\u7372\u5f97\u7f8e\u570b\u5c0d\u9019\u4e00\u57fa\u56e0\u7de8\u8f2f\u7642\u6cd5\u7684\u6279\u51c6\u3002<\/p>\n<p>\u6240\u4ee5\u4eca\u5929\u8981\u8ac7\u8ad6\u7684\u662fCRISPR Therapeutics\u80a1\u7968\u4ee5\u53ca\u89e3\u91cb\u70ba\u4ec0\u9ebc\u8a72\u80a1\u6703\u8d70\u9ad8\u3002<\/p>\n<h2>CRISPR Therapeutics\u80fd\u505a\u4ec0\u9ebc<\/h2>\n<p>CRISPR Therapeutics\u662f\u4e00\u5bb6\u81e8\u5e8a\u968e\u6bb5\u7684\u751f\u7269\u79d1\u6280\u516c\u53f8\uff0c\u5229\u7528CRISPR-Cas9\u57fa\u56e0\u7de8\u8f2f\u7cfb\u7d71\u958b\u767c\u91dd\u5c0d\u5305\u62ec\u907a\u50b3\u6027\u8840\u6db2\u75c5\u548c\u764c\u75c7\u5728\u5167\u7684\u4e00\u7cfb\u5217\u75be\u75c5\u7684\u7642\u6cd5\u3002\u6838\u5fc3\u662f\u57fa\u56e0\u7de8\u8f2f\u6280\u8853\uff0c\u9019\u4f7f\u5f97\u79d1\u5b78\u5bb6\u80fd\u5920\u7cbe\u78ba\u5730\u4fee\u6539\u548c\u7de8\u8f2f\u751f\u7269\u9ad4\u5167\u7684\u57fa\u56e0\uff0c\u5f9e\u800c\u6709\u53ef\u80fd\u5fb9\u5e95\u6539\u8b8a\u907a\u50b3\u75be\u75c5\u7684\u6cbb\u7642\u3002<\/p>\n<p>CRISPR Therapeutics\u7684\u4e00\u500b\u91cd\u9ede\u65b9\u5411\u662f\u907a\u50b3\u6027\u8840\u6db2\u75c5\u3002\u901a\u904e\u63a1\u7528CRISPR-Cas9\uff0c\u8a72\u516c\u53f8\u65e8\u5728\u958b\u767c\u80fd\u5920\u7cfe\u6b63\u6216\u8abf\u7bc0\u5c0e\u81f4\u9019\u4e9b\u75be\u75c5\u7684\u57fa\u56e0\u7a81\u8b8a\u7684\u9776\u5411\u7642\u6cd5\uff0c\u5f9e\u800c\u70ba\u66f4\u6709\u6548\u548c\u500b\u6027\u5316\u7684\u6cbb\u7642\u63d0\u4f9b\u6f5b\u529b\u3002<\/p>\n<p>\u5728\u764c\u75c7\u9818\u57df\uff0c\u8a72\u516c\u53f8\u6b63\u5728\u63a2\u7d22\u57fa\u56e0\u7de8\u8f2f\u7684\u61c9\u7528\u4f86\u958b\u767c\u5275\u65b0\u7642\u6cd5\u3002CRISPR-Cas9\u7684\u7cbe\u78ba\u6027\u4f7f\u79d1\u5b78\u5bb6\u80fd\u5920\u9776\u5411\u548c\u4fee\u6539\u8207\u764c\u75c7\u9032\u5c55\u76f8\u95dc\u7684\u7279\u5b9a\u57fa\u56e0\uff0c\u5f9e\u800c\u6709\u53ef\u80fd\u7834\u58de\u816b\u7624\u751f\u9577\u6a5f\u5236\u3002<\/p>\n<h2>\u6700\u65b0\u52d5\u614b<\/h2>\n<p>\u82f1\u570b\u6279\u51c6exa-cel\u6cbb\u7642\u942e\u72c0\u7d30\u80de\u75c5(SCD)\u548c\u8f38\u8840\u4f9d\u8cf4\u6027\u03b2\u5730\u4e2d\u6d77\u8ca7\u8840(TDT)\uff0c\u9019\u53ea\u662f\u958b\u59cb\u3002\u6b64\u6b21\u6279\u51c6\u4e0d\u50c5\u5c0dCRISPR Therapeutics\u4f86\u8aaa\u662f\u4e00\u500b\u91cc\u7a0b\u7891\u6642\u523b\uff08exa-cel\u662fCRISPR Therapeutics\u7684\u9996\u6b3e\u7522\u54c1\uff09\uff0c\u4e5f\u662f\u4e16\u754c\u4e0a\u7b2c\u4e00\u500b\u7372\u6279\u7684\u57fa\u56e0\u7de8\u8f2f\u7642\u6cd5\u3002\u9019\u4e5f\u70ba\u5728\u4e16\u754c\u5176\u4ed6\u5730\u65b9\u7372\u5f97\u76e3\u7ba1\u6279\u51c6\u92ea\u5e73\u4e86\u9053\u8def\uff0c\u5c24\u5176\u662f\u5728\u7f8e\u570b\uff0c\u76e3\u7ba1\u6279\u51c6\u5df2\u7d93\u63a5\u8fd1\u5c3e\u8072\u3002<\/p>\n<h2>\u6578\u64da<\/h2>\n<p>\u8a72\u7642\u6cd5\u5728\u81e8\u5e8a\u8a66\u9a57\u4e2d\u986f\u793a\u51fa\u5f15\u4eba\u6ce8\u76ee\u7684\u7642\u6548\u3002\u8a66\u9a57\u4e2d\u9664\u4e00\u540d\u60a3\u8005\u5916\uff0c\u6240\u6709\u60a3\u8005\u5728\u4ee4\u4eba\u6eff\u610f\u7684\u89c0\u5bdf\u671f\u5f8c\uff0c\u75be\u75c5\u5df2\u5f97\u5230\u529f\u80fd\u6027\u6cbb\u7652\u3002<\/p>\n<p>\u7f8e\u570b\u670910\u842c\u4eba\u88ab\u8a3a\u65b7\u60a3\u6709\u9019\u7a2e\u75be\u75c5\uff0c\u4e16\u754c\u5176\u4ed6\u5730\u65b9\u67092\u842c\u4eba\u88ab\u8a3a\u65b7\u60a3\u6709\u9019\u7a2e\u75be\u75c5\u3002\u5118\u7ba1\u6f5b\u5728\u60a3\u8005\u6578\u91cf\u773e\u591a\uff0c\u4f46\u5206\u6790\u5e2b\u9810\u8a08\u521d\u59cb\u60a3\u8005\u4eba\u6578\u5c07\u63a5\u8fd120,000\u4eba\uff0c\u50f9\u683c\u7d04\u70ba200\u842c\u7f8e\u5143\u3002\u9019\u610f\u5473\u8457\u9ad8\u9054400\u5104\u7f8e\u5143\u7684\u5de8\u5927\u92b7\u552e\u984d\uff0c\u5176\u4e2dCRISPR Therapeutics\u5206\u621040%\uff0cVertex\u5206\u621060%\u3002<\/p>\n","protected":false},"excerpt":{"rendered":"<p>11\u670816\u65e5\uff0c\u82f1\u570b\u85e5\u54c1\u76e3\u7ba1\u6a5f\u69cb\u6279\u51c6\u4e86\u4e00\u7a2e\u4f7f\u7528CRISPR-Cas9\u57fa\u56e0\u7de8\u8f2f\u5de5\u5177\u7684\u7642\u6cd5\u3002\u9019\u4f7f\u6210\u9577\u80a1CRISPR  [&hellip;]<\/p>\n","protected":false},"author":9,"featured_media":478972,"comment_status":"closed","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"footnotes":"","_links_to":"","_links_to_target":""},"categories":[426],"tags":[809,2156,644,564],"class_list":["post-478974","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-market-news-zh-hant","tag-809","tag-2156","tag-644","tag-564","sectors-life-science-zh-hant","locations-us-zh-hant","exchange-nasdaq-zh-hant","exchange-nyse-zh-hant"],"acf":[],"_links":{"self":[{"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/posts\/478974","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/users\/9"}],"replies":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/comments?post=478974"}],"version-history":[{"count":0,"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/posts\/478974\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/media\/478972"}],"wp:attachment":[{"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/media?parent=478974"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/categories?post=478974"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/nai500.com\/zh-hant\/wp-json\/wp\/v2\/tags?post=478974"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}