{"id":544749,"date":"2024-07-03T19:09:32","date_gmt":"2024-07-04T02:09:32","guid":{"rendered":"https:\/\/nai500.com\/blog\/2024\/07\/%e4%bd%8e%e4%b9%b0%e9%ab%98%e5%8d%96%ef%bc%8c%e4%b8%8d%e9%80%82%e7%94%a8%e4%ba%8e%e8%bf%99%e5%8f%aa%e7%94%9f%e7%89%a9%e7%a7%91%e6%8a%80%e8%82%a1%e7%a5%a8\/"},"modified":"2024-07-03T19:10:10","modified_gmt":"2024-07-04T02:10:10","slug":"%e4%bd%8e%e8%b2%b7%e9%ab%98%e8%b3%a3%ef%bc%8c%e4%b8%8d%e9%81%a9%e7%94%a8%e6%96%bc%e9%80%99%e5%8f%aa%e7%94%9f%e7%89%a9%e7%a7%91%e6%8a%80%e8%82%a1%e7%a5%a8","status":"publish","type":"post","link":"https:\/\/nai500.com\/zh-hant\/blog\/2024\/07\/%e4%bd%8e%e8%b2%b7%e9%ab%98%e8%b3%a3%ef%bc%8c%e4%b8%8d%e9%81%a9%e7%94%a8%e6%96%bc%e9%80%99%e5%8f%aa%e7%94%9f%e7%89%a9%e7%a7%91%e6%8a%80%e8%82%a1%e7%a5%a8\/","title":{"rendered":"\u4f4e\u8cb7\u9ad8\u8ce3\uff0c\u4e0d\u9069\u7528\u65bc\u9019\u53ea\u751f\u7269\u79d1\u6280\u80a1\u7968"},"content":{"rendered":"<p>\u201c\u4f4e\u8cb7\u9ad8\u8ce3\u201d\uff0c\u9019\u662f\u6700\u7c21\u55ae\u4f46\u4e5f\u662f\u6700\u96e3\u7684\u6295\u8cc7\u6210\u529f\u6cd5\u5247\u3002\u8aaa\u7c21\u55ae\uff0c\u8ab0\u90fd\u807d\u5f97\u61c2\uff0c\u8aaa\u96e3\uff0c\u5177\u9ad4\u64cd\u4f5c\u6642\u5e02\u5834\u6839\u672c\u201c\u4e0d\u914d\u5408\u4f60\u201d\uff0c\u751a\u81f3\u8ddf\u4f60\u201c\u5c0d\u8457\u5e79\u201d\u3002\u8209\u4f8b\u4f86\u8aaa\uff0c\u6709\u4e9b\u5f37\u52e2\u500b\u80a1\u6f32\u5e45\u5df2\u7d93\u4e0d\u5c0f\uff0c\u4f46\u672a\u4f86\u9084\u6709\u7e7c\u7e8c\u4e0a\u6f32\u7684\u7a7a\u9593\uff0c\u9019\u6642\u5019\u5c31\u4e0d\u80fd\u7b49\u5f85\u80a1\u50f9\u56de\u8abf\u5f8c\u518d\u8cb7\u5165\uff0c\u611a\u5b88\u201c\u4f4e\u8cb7\u9ad8\u8ce3\u201d\u7684\u539f\u5247\uff0c\u800c\u662f\u61c9\u8a72\u5927\u81bd\u201c\u9ad8\u8cb7\u201d\u3002<\/p>\n<p>\u751f\u7269\u79d1\u6280\u516c\u53f8<a href=\"https:\/\/nai500.com\/zh-hans\/%e8%82%a1%e7%a5%a8%e6%9f%a5%e8%af%a2\/?qm_symbol=SRPT\">Sarepta Therapeutics Inc\uff08NASDAQ:SRPT\uff09<\/a>\u5c31\u662f\u9019\u6a23\u7684\u4e00\u96bb\u80a1\u7968\u3002\u8a72\u80a1\u80a1\u50f9\u4eca\u5e74\u8fc4\u4eca\u5df2\u7d93\u5927\u6f3262%\uff0c\u4f46\u80a1\u50f9\u5c1a\u672a\u89f8\u9802\uff0c\u751a\u81f3\u9069\u5408\u9577\u7dda\u6301\u6709\u3002<\/p>\n<h2>Sarepta\u7684\u6bba\u624b\u9427\uff1aElevidys<\/h2>\n<p>\u5230\u76ee\u524d\u70ba\u6b62\uff0cSarepta Therapeutics\u6700\u91cd\u8981\u7684\u4e0a\u5e02\u7522\u54c1\u662fElevidys\u3002\u9019\u662f\u8a72\u516c\u53f8\u806f\u5408\u7f85\u6c0f\u958b\u767c\u4e26\u5728\u53bb\u5e746\u6708\u7372\u6279\u7684\u675c\u6c0f\u808c\u71df\u990a\u4e0d\u826f\u75c7\uff08DMD\uff09\u85e5\u54c1\uff0c\u540c\u6642\u4e5f\u662f\u7b2c\u4e00\u6b3e\u7372\u6279\u7684DMD\u57fa\u56e0\u7642\u6cd5\u3002<\/p>\n<p>Elevidys\u53bb\u5e74\u5728\u7f8e\u7372\u5f97\u52a0\u901f\u6279\u51c6\uff0c\u9019\u610f\u5473\u8457Sarepta Therapeutics\u5fc5\u9808\u958b\u5c55\u4e0a\u5e02\u5f8c\u7814\u7a76\u4ee5\u8b49\u660e\u5b83\u7684\u6709\u6548\u6027\u3002\u5f8c\u7e8c\u8a66\u9a57\u96d6\u7136\u6c92\u80fd\u9054\u6210\u4e3b\u8981\u7d42\u9ede\uff0c\u4f46\u9054\u5230\u4e86\u6240\u6709\u7684\u6b21\u8981\u7d42\u9ede\u3002\u56e0\u6b64\uff0cSarepta\u7533\u8acb\u64f4\u5927\u6279\u51c6\uff0cElevidys\u76ee\u524d\u5df2\u7372\u7121\u5e74\u9f61\u9650\u5236\uff08\u6b64\u524d\u50c5\u9650\u65bc4-5\u6b72\uff09\u975e\u81e5\u5e8a\u60a3\u8005\u7684\u5b8c\u5168\u6279\u51c6\uff0c\u4ee5\u53ca\u81e5\u5e8a\u60a3\u8005\u7684\u52a0\u901f\u6279\u51c6\u3002\u7c21\u55ae\u4f86\u8aaa\uff0cElevidys\u7684\u5e02\u5834\u6f5b\u529b\u73fe\u5728\u8b8a\u5f97\u66f4\u5927\u4e86\u3002<\/p>\n<p>Sarepta Therapeutics\u7684\u8ca1\u52d9\u548c\u696d\u7e3e\u4e5f\u5728\u5411\u597d\u3002\u516c\u53f8\u4e00\u5b63\u5ea6\u7e3d\u6536\u5165\u540c\u6bd4\u589e\u957763%\u81f34.135\u5104\u7f8e\u5143\uff0c\u5176\u4e2dElevidys\u7684\u7522\u54c1\u6536\u5165\u90541.339\u5104\u7f8e\u5143\u3002\u6b64\u5916\uff0c\u8a72\u516c\u53f8\u7d42\u65bc\u626d\u8667\u70ba\u76c8\uff0c\u5f9e\u4e0a\u5e74\u540c\u671f\u7684\u8abf\u6574\u5f8c\u6bcf\u80a1\u8667\u640d0.99\u7f8e\u5143\u8f49\u70ba\u8abf\u6574\u5f8c\u6bcf\u80a1\u6de8\u52290.73\u7f8e\u5143\u3002<\/p>\n<h2>\u9019\u53ea\u751f\u7269\u79d1\u6280\u80a1\u7684\u660e\u5929\u6703\u66f4\u597d<\/h2>\n<p>Sarepta Therapeutics\u672a\u4f86\u5e7e\u500b\u5b63\u5ea6\u7684\u6536\u5165\u589e\u901f\u5c07\u6703\u66f4\u9ad8\u3002\u8a72\u516c\u53f8\u4f30\u7b97Elevidys\u7684\u5e74\u5ea6\u5cf0\u503c\u92b7\u552e\u984d\u7d04\u70ba40\u5104\u7f8e\u5143\uff0cNeedham &amp; 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